Condition
Inherited BMF Syndrome clinical trials and research
As of November 12, 2026, Find a Trial lists 4 Inherited BMF Syndrome clinical trials that are recruiting, at sites in 3 countries (most in United States (2), Egypt (1), Australia (1)). By phase: Phase 1/2 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 4Clinical trials
- 3Countries
Newest Inherited BMF Syndrome clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| Global Shwachman-Diamond Syndrome Patient Survey and Collaboration Platform | — | Woburn, Massachusetts | Recruiting | May 31, 2025 |
| Using CD45RA Depleted Stem Cells to Prevent Infections After Transplant | Phase 1/2 | Philadelphia, Pennsylvania | Recruiting | Feb 21, 2025 |
| Exploring genetic causes of inherited bone marrow failure syndromes | — | Sohag | Recruiting | Jun 29, 2022 |
| Genomic analysis for patients with inherited bone marrow failure | — | Melbourne, Victoria | Recruiting | Jan 19, 2022 |
All recruiting trials (4)
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Global Shwachman-Diamond Syndrome Patient Survey and Collaboration Platform
An online program for people with Shwachman-Diamond Syndrome and their families to share health experiences, join a global community, and receive early information about research and clinical opportunities.
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Using CD45RA Depleted Stem Cells to Prevent Infections After Transplant
This study is testing whether using special stem cells can help patients with high-risk leukemia recover their immune system faster and prevent infections after a stem cell transplant.
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Exploring genetic causes of inherited bone marrow failure syndromes
This study is testing the genetic causes of inherited bone marrow failure syndromes to help improve diagnosis and treatment for people with these conditions.
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Genomic analysis for patients with inherited bone marrow failure
This study is testing if advanced genetic testing can help identify the causes of inherited bone marrow failure in patients, so they can get better treatment and support.
Related topics
Quick answers
How many Inherited BMF Syndrome clinical trials are recruiting right now?
4, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 3 countries. The most sites are in United States (2 trials), Egypt (1 trial), Australia (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1/2: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.