Patchy (mosaic) genetic changes in focal epilepsy

Human Epilepsy Genetics - Mosaic Mutations in Focal Epilepsy

NIH-funded research Boston Children's Hospital · NIH-11238895

This project looks for mosaic (patchy) genetic mutations in brain tissue from people with mesial temporal lobe epilepsy to better understand causes and help guide future treatment choices.

Quick facts

Grant typeR37 grant
Study typeNIH-funded research
Funding institutionBoston Children's Hospital NIH-funded
Lab location1 site (Boston, United States)
Project IDNIH-11238895 on NIH RePORTER

What this research studies

I would be asked whether genetic changes that occur in only some brain cells help cause focal mesial temporal lobe epilepsy (mTLE). Researchers sequence DNA from brain tissue removed during epilepsy surgery and compare it to blood to find mutations that are only in the brain. They focus on genes in the RAS signaling pathway but will look more broadly to find other genetic regulators. The team will analyze many more resected samples to confirm earlier findings and to see if specific mutations relate to outcomes and treatment options.

Who could benefit from this research

Good fit: Ideal candidates are adolescents and adults with medically refractory mesial temporal lobe epilepsy who are undergoing or have had brain tissue resected for seizure control.

Not a fit: People with generalized epilepsy, those whose seizures are well controlled by medication, or individuals not having brain surgery are unlikely to receive direct benefit from participation.

Why it matters

Potential benefit: If successful, this work could explain why some focal epilepsies are resistant to drugs and point toward more targeted treatments or better surgical decisions.

How similar studies have performed: Earlier small studies of resected epilepsy tissue have found somatic RAS-pathway mutations in some cases, so these results extend promising but still early findings.

Where this research is happening

Boston, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Candidate Disease Gene
Last reviewed 2026-06-09 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.