Condition
Tay-Sachs Disease clinical trials and research
As of November 12, 2026, Find a Trial lists 3 Tay-Sachs Disease clinical trials that are recruiting, in United States. By phase: Phase 1 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 3Clinical trials
- 1Country
Newest Tay-Sachs Disease clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| Long-term observation of rare genetic brain disorders | — | Pittsburgh, Pennsylvania | Recruiting | Nov 6, 2017 |
| Using umbilical cord blood cells to treat inherited metabolic diseases | Phase 1 | Durham, North Carolina | Recruiting | Oct 2, 2014 |
| Understanding the progression of gangliosidosis diseases | — | Minneapolis, Minnesota | Recruiting | Apr 29, 2008 |
All recruiting trials (3)
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Long-term observation of rare genetic brain disorders
This study is tracking how rare genetic brain disorders progress over time to better understand their effects on patients.
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Using umbilical cord blood cells to treat inherited metabolic diseases
This study is testing if a new treatment using special cells from umbilical cord blood can help people with inherited metabolic diseases and early signs of nerve damage feel better when combined with standard cord blood transplants.
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Understanding the progression of gangliosidosis diseases
This study looks at how gangliosidosis diseases, like Tay-Sachs and Sandhoff, progress over time in order to help doctors and families understand the conditions better and prepare for future treatments.
Related topics
Quick answers
How many Tay-Sachs Disease clinical trials are recruiting right now?
3, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
All of them have sites in United States. Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.