Condition
MPS I clinical trials and research
As of November 12, 2026, Find a Trial lists 3 MPS I clinical trials that are recruiting, in United States. By phase: Phase 1 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 3Clinical trials
- 1Country
Newest MPS I clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| Heart and blood vessel changes in mucopolysaccharidosis (MPS) | — | Orange, California and 2 other locations | Recruiting | Jan 23, 2026 |
| In utero enzyme replacement therapy for lysosomal storage disorders | Phase 1 | San Francisco, California | Recruiting | Aug 31, 2020 |
| Long-term observation of rare genetic brain disorders | — | Pittsburgh, Pennsylvania | Recruiting | Nov 6, 2017 |
All recruiting trials (3)
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Heart and blood vessel changes in mucopolysaccharidosis (MPS)
This project will see if people with mucopolysaccharidosis (MPS) have faster artery thickening or stiffening and different blood or urine markers linked to heart and vessel problems than people without MPS.
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In utero enzyme replacement therapy for lysosomal storage disorders
This study is testing whether giving enzyme replacement therapy to unborn babies with lysosomal storage disorders can improve their health and development before they are born.
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Long-term observation of rare genetic brain disorders
This study is tracking how rare genetic brain disorders progress over time to better understand their effects on patients.
Related topics
Quick answers
How many MPS I clinical trials are recruiting right now?
3, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
All of them have sites in United States. Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.