Condition
Vanishing White Matter Disease clinical trials and research
As of November 12, 2026, Find a Trial lists 3 Vanishing White Matter Disease clinical trials that are recruiting, at sites in 3 countries (most in United States (3), Canada (1), Netherlands (1)). By phase: Phase 1/2 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 3Clinical trials
- 3Countries
Newest Vanishing White Matter Disease clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| Exploring Fosigotifator for Vanishing White Matter Disease | Phase 1/2 | Boston, Massachusetts and 4 other locations | Recruiting | Mar 7, 2023 |
| Long-term observation of rare genetic brain disorders | — | Pittsburgh, Pennsylvania | Recruiting | Nov 6, 2017 |
| Collecting data and samples from patients with leukodystrophy | — | Los Angeles, California and 22 other locations | Recruiting | Feb 9, 2017 |
All recruiting trials (3)
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Exploring Fosigotifator for Vanishing White Matter Disease
This study is testing a new drug called Fosigotifator to see if it can help people of all ages with Vanishing White Matter disease feel better and stay healthy.
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Long-term observation of rare genetic brain disorders
This study is tracking how rare genetic brain disorders progress over time to better understand their effects on patients.
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Collecting data and samples from patients with leukodystrophy
This study is collecting health information and samples from people with leukodystrophy to help find new causes and better treatments for the condition.
Related topics
Quick answers
How many Vanishing White Matter Disease clinical trials are recruiting right now?
3, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 3 countries. The most sites are in United States (3 trials), Canada (1 trial), Netherlands (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1/2: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.