Condition
Mucopolysaccharidosis II clinical trials and research
As of November 12, 2026, Find a Trial lists 3 Mucopolysaccharidosis II clinical trials that are recruiting, at sites in 2 countries (most in United States (2), France (1)). By phase: Phase 1 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 3Clinical trials
- 2Countries
Newest Mucopolysaccharidosis II clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| Observational study on Mucopolysaccharidosis diseases in France | — | Angers and 22 other locations | Recruiting | Sep 14, 2023 |
| Registry for patients with lysosomal storage diseases | — | San Francisco, California | Recruiting | Nov 17, 2022 |
| Using umbilical cord blood cells to treat inherited metabolic diseases | Phase 1 | Durham, North Carolina | Recruiting | Oct 2, 2014 |
All recruiting trials (3)
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Observational study on Mucopolysaccharidosis diseases in France
This study is trying to learn more about Mucopolysaccharidosis diseases by collecting information from patients in France to understand how these rare conditions affect their lives.
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Registry for patients with lysosomal storage diseases
This study is collecting information from patients with lysosomal storage diseases to see how these conditions progress and how treatments can improve care for them and their families.
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Using umbilical cord blood cells to treat inherited metabolic diseases
This study is testing if a new treatment using special cells from umbilical cord blood can help people with inherited metabolic diseases and early signs of nerve damage feel better when combined with standard cord blood transplants.
Related topics
Quick answers
How many Mucopolysaccharidosis II clinical trials are recruiting right now?
3, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 2 countries. The most sites are in United States (2 trials), France (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.