Condition
Niemann-Pick Diseases clinical trials and research
As of November 12, 2026, Find a Trial lists 3 Niemann-Pick Diseases clinical trials that are recruiting, at sites in 2 countries (most in United States (2), Australia (1)). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 3Clinical trials
- 2Countries
Newest Niemann-Pick Diseases clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| Hyperspectral retinal imaging to detect Alzheimer’s and other neurodegenerative changes | — | Melbourne, Victoria | Recruiting | Apr 22, 2026 |
| Long-term safety and immune response of olipudase alfa in young children with acid sphingomyelinase deficiency | — | Chicago, Illinois and 5 other locations | Recruiting | Jan 5, 2024 |
| Long-term observation of rare genetic brain disorders | — | Pittsburgh, Pennsylvania | Recruiting | Nov 6, 2017 |
All recruiting trials (3)
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Hyperspectral retinal imaging to detect Alzheimer’s and other neurodegenerative changes
This project will test whether a special retinal camera that scans many wavelengths of light can detect signs of Alzheimer’s and other neurodegenerative diseases in people with dementia or at risk.
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Long-term safety and immune response of olipudase alfa in young children with acid sphingomyelinase deficiency
This study is testing the long-term safety and immune response of a treatment called olipudase alfa in young children under 2 years old who have acid sphingomyelinase deficiency.
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Long-term observation of rare genetic brain disorders
This study is tracking how rare genetic brain disorders progress over time to better understand their effects on patients.
Related topics
Quick answers
How many Niemann-Pick Diseases clinical trials are recruiting right now?
3, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 2 countries. The most sites are in United States (2 trials), Australia (1 trial). Each study page lists its sites and which ones are recruiting.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.