Condition
Lysosomal Storage Diseases clinical trials and research
As of November 12, 2026, Find a Trial lists 2 Lysosomal Storage Diseases clinical trials that are recruiting, at sites in 2 countries (most in United States (1), France (1)). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 2Clinical trials
- 2Countries
All recruiting trials (2)
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Systematic newborn screening for lysosomal storage diseases using mass spectrometry in Normandy
This project will test a mass spectrometry blood screening for MPS I and Pompe disease in newborns born in Normandy to see how many cases are found.
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Long-term observation of rare genetic brain disorders
This study is tracking how rare genetic brain disorders progress over time to better understand their effects on patients.
Related topics
Quick answers
How many Lysosomal Storage Diseases clinical trials are recruiting right now?
2, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 2 countries. The most sites are in United States (1 trial), France (1 trial). Each study page lists its sites and which ones are recruiting.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.