Training program for muscle disease research and treatment
Official title: MDSRC Training Core
Funded at Research Inst Nationwide Children's Hosp · NIH-10992524 · Data updated 2026-11-12
This study is all about training a new generation of students and early-career doctors to better understand and treat muscle diseases, especially neuromuscular disorders, through hands-on workshops and mentorship at Nationwide Children’s Hospital and The Ohio State University.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Research Inst Nationwide Children's Hosp NIH-funded |
| Lab location | 1 site (Columbus, United States) |
| Project start | August 15, 2024 |
| Project end | July 31, 2028 |
| Funding year | 2024 |
| Award (this year) | $148,896 |
| NIH project number | 1P50HD117373-01A1 |
| Project ID | NIH-10992524 on NIH RePORTER |
Who could benefit from this research
✓Could help
Ideal candidates for participation or benefit from this research include students and early-career professionals interested in neuromuscular diseases and gene therapy.
✕Less likely to help
Patients who are not involved in educational or training programs related to muscle diseases may not receive direct benefits from this research.
What this research studies
This research focuses on creating a robust training environment for understanding and treating muscle diseases, particularly neuromuscular disorders, at Nationwide Children’s Hospital and The Ohio State University. It aims to educate a diverse group of trainees, including high school students, undergraduates, and early-stage physician scientists, through various programs designed to enhance their skills and knowledge in gene therapy and muscle health. The initiative includes hands-on workshops, mentorship, and collaborative opportunities with leading scientists and clinicians in the field. By fostering a new generation of researchers and clinicians, the program seeks to advance the understanding and treatment of muscle diseases.
Why it matters
Potential benefit: If successful, this research could lead to improved treatment options and outcomes for patients with muscle diseases through enhanced training of future healthcare professionals.
How similar studies have gone: Previous initiatives in similar training environments have shown success in advancing knowledge and treatment options in the field of muscle diseases.
Where this research is happening
-
Research Inst Nationwide Children's Hosp
Columbus, United States Active
Researchers
- Principal investigator: Harper, Scott Q — Research Inst Nationwide Children's Hosp
- Study coordinator: Harper, Scott Q
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About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page.