Condition
Bone Marrow Failure Syndrome clinical trials and research
As of November 12, 2026, Find a Trial lists 6 Bone Marrow Failure Syndrome clinical trials that are recruiting, at sites in 3 countries (most in United States (4), China (1), France (1)). By phase: Phase 2 (2), Phase 1 (1), Early Phase 1 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 6Clinical trials
- 3Countries
Newest Bone Marrow Failure Syndrome clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| Stem cell mobilization and collection for life-threatening blood disorders | Phase 1 | Memphis, Tennessee | Recruiting | May 13, 2026 |
| CD7 CAR-T cell treatment for blood and immune system diseases | Early Phase 1 | Hangzhou, Zhejiang | Recruiting | Jan 22, 2025 |
| National registry for patients with bone marrow failure syndromes in France | — | Paris | Recruiting | Mar 4, 2021 |
| Haploidentical transplant for severe aplastic anemia | Phase 2 | Memphis, Tennessee | Recruiting | Sep 22, 2020 |
| Haploidentical stem cell transplant for treating blood disorders in children | Phase 2 | St. Petersburg, Florida | Recruiting | Apr 22, 2020 |
| Testing genetic markers for early detection of myeloid cancers and bone marrow failure | — | Scottsdale, Arizona and 2 other locations | Recruiting | Nov 8, 2016 |
All recruiting trials (6)
-
Stem cell mobilization and collection for life-threatening blood disorders
This study tests a FIlgrastim plus plerixafor approach to safely mobilize and collect stem cells from adults with bone marrow failure for potential gene therapy.
-
CD7 CAR-T cell treatment for blood and immune system diseases
This study is testing a new CAR-T cell treatment combined with stem cell transplants to see if it can help people with certain blood and immune system diseases feel better.
-
National registry for patients with bone marrow failure syndromes in France
This study is collecting health information and samples from patients with bone marrow failure syndromes in France to better understand these rare diseases and improve their treatment.
-
Haploidentical transplant for severe aplastic anemia
This study is testing a new type of stem cell transplant for people with severe aplastic anemia to see if it can help them recover better and reduce the risk of complications.
-
Haploidentical stem cell transplant for treating blood disorders in children
This study is testing a new way to use stem cell transplants from partially matched family members to help children with serious blood disorders feel better when other treatments haven't worked.
-
Testing genetic markers for early detection of myeloid cancers and bone marrow failure
This study is testing if looking for specific genetic markers in blood and tissue samples can help find myeloid cancers and bone marrow issues earlier in people who show early signs but aren't diagnosed yet.
Related topics
Quick answers
How many Bone Marrow Failure Syndrome clinical trials are recruiting right now?
6, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 3 countries. The most sites are in United States (4 trials), China (1 trial), France (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 2: 2, Phase 1: 1, Early Phase 1: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.