Condition
Inherited Bone Marrow Failure Syndrome clinical trials and research
As of November 12, 2026, Find a Trial lists 4 Inherited Bone Marrow Failure Syndrome clinical trials that are recruiting, at sites in 2 countries (most in United States (3), Italy (1)). 1 was first registered in the last 30 days. By phase: Phase 1 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 4Clinical trials
- 1New in 30 days
- 2Countries
Newest Inherited Bone Marrow Failure Syndrome clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| Understanding congenital bone marrow failure and related disorders through a national network | — | Avellino and 3 other locations | Recruiting | Oct 16, 2026 |
| Using imatinib to enhance RUNX1 activity in patients with RUNX1 mutations | Phase 1 | Bethesda, Maryland | Recruiting | Oct 19, 2023 |
| Understanding Squamous Cell Carcinoma in People with Fanconi Anemia | — | Bethesda, Maryland | Recruiting | Jan 18, 2023 |
| Testing genetic markers for early detection of myeloid cancers and bone marrow failure | — | Scottsdale, Arizona and 2 other locations | Recruiting | Nov 8, 2016 |
All recruiting trials (4)
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Understanding congenital bone marrow failure and related disorders through a national network
This project tests whether people with rare inherited bone marrow failure syndromes or related conditions really have the underlying genetic causes, by collecting data and samples across multiple centers.
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Using imatinib to enhance RUNX1 activity in patients with RUNX1 mutations
This study is testing if the medication imatinib can help people with RUNX1 mutations feel better and improve their bone marrow function.
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Understanding Squamous Cell Carcinoma in People with Fanconi Anemia
This study looks at how squamous cell carcinoma develops in people with Fanconi anemia to help catch it early and improve treatment options.
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Testing genetic markers for early detection of myeloid cancers and bone marrow failure
This study is testing if looking for specific genetic markers in blood and tissue samples can help find myeloid cancers and bone marrow issues earlier in people who show early signs but aren't diagnosed yet.
Related topics
Quick answers
How many Inherited Bone Marrow Failure Syndrome clinical trials are recruiting right now?
4, as of November 12, 2026. 1 of them was first registered in the last 30 days. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 2 countries. The most sites are in United States (3 trials), Italy (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.