Using post-transplant cyclophosphamide and ATG for blood cancer transplants

Efficacy Evaluation of Post-transplant Cyclophosphamide-based Graft-versus-host Disease Prophylaxis with ATG, Calcineurin Inhibitor-free, for Matched-sibling or Matched-unrelated Transplantation

PHASE1; PHASE2 · Instituto Nacional de Cancer, Brazil · NCT06299462

This study is testing whether using post-transplant cyclophosphamide and ATG can help prevent graft-versus-host disease in patients with blood cancers who are getting stem cell transplants.

Quick facts

PhasePHASE1; PHASE2
Study typeInterventional
Enrollment50 (estimated)
Ages18 Years to 60 Years
SexAll
SponsorInstituto Nacional de Cancer, Brazil (other gov)
Drugs / interventionscyclophosphamide
Locations1 site (Rio de Janeiro, Rio de Janeiro)
Trial IDNCT06299462 on ClinicalTrials.gov

What this trial studies

This clinical trial investigates the use of post-transplant cyclophosphamide and anti-thymocyte globulin (ATG) as a prophylactic treatment to prevent graft-versus-host disease (GVHD) in patients undergoing hematopoietic stem cell transplantation. The study focuses on patients with acute leukemia, myelodysplastic syndromes, and lymphomas who are receiving related or unrelated HLA-compatible transplants. It aims to evaluate the effectiveness of this approach compared to traditional calcineurin inhibitors, which have a poorer toxicity profile. The trial is designed as a prospective, two-arm, non-randomized study.

Who should consider this trial

Good fit: Ideal candidates for this study are adults aged 18 to 60 with specific types of blood cancers in remission who are eligible for HLA-compatible stem cell transplants.

Not a fit: Patients with hepatic dysfunction or those outside the specified age range may not benefit from this study.

Why it matters

Potential benefit: If successful, this approach could significantly reduce the incidence of graft-versus-host disease in transplant patients, improving their overall outcomes.

How similar studies have performed: Previous studies have shown success with post-transplant cyclophosphamide in haploidentical transplants, suggesting potential for similar benefits in matched transplants.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Patient with (1) acute leukemia in first or second remission; (2) myelodysplasia with less than 20% blasts; (3) Hodgkin's or non-Hodgkin's lymphoma, in partial remission after salvage therapy
* Who will receive a related or unrelated, HLA-compatible transplant;
* Who is a transplant candidate with FluMel, FluTBI, CyTBI, BuCy or BuFlu conditioning;
* Peripheral blood source;
* Age between 18 and 60 years.

Exclusion Criteria:

\- Hepatic dysfunction (transaminases x2 the normal value)

Where this trial is running

Rio de Janeiro, Rio de Janeiro

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.

View on ClinicalTrials.gov →

Conditions: Acute Myeloid Leukemia, Acute Lymphoblastic Leukemia, Myelodysplastic Syndromes, Hodgkin Lymphoma, Non-hodgkin Lymphoma, posttransplant cyclophosphamide, ATG, calcineurin-free GVHD prophylaxis

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.