Using cyclophosphamide for bone marrow transplants from unrelated donors

Use of Post Transplant Cyclophosphamide as Graft Versus Host Disease Prophylaxis in Matched Unrelated Donor Stem Cell Transplantation for Hematological Malignancies, a Prospective Randomized Controlled Trial

PHASE2; PHASE3 · Hospital Israelita Albert Einstein · NCT03818334

This study is testing if using cyclophosphamide can help people who get bone marrow transplants from unrelated donors live longer and have fewer complications.

Quick facts

PhasePHASE2; PHASE3
Study typeInterventional
Enrollment50 (estimated)
Ages1 Year to 75 Years
SexAll
SponsorHospital Israelita Albert Einstein (other)
Drugs / interventionscyclophosphamide
Locations1 site (São Paulo, São Paulo)
Trial IDNCT03818334 on ClinicalTrials.gov

What this trial studies

This study evaluates the effectiveness of cyclophosphamide in improving survival rates and reducing complications in patients receiving bone marrow transplants from matched unrelated donors. A total of fifty participants will be enrolled, with thirty receiving cyclophosphamide and twenty receiving antihuman T-lymphocyte immune globulin (ATG). The primary focus is on overall survival, progression-free survival, and the incidence of acute and chronic graft-versus-host disease (GvHD). The study aims to provide insights into the best post-transplant care for patients with hematological malignancies.

Who should consider this trial

Good fit: Ideal candidates include men and women of any age with hematological malignancies who require a stem cell transplant from a matched unrelated donor.

Not a fit: Patients with acute leukemias not in complete response or those with severe organ dysfunction may not benefit from this study.

Why it matters

Potential benefit: If successful, this approach could significantly improve survival rates and reduce complications for patients undergoing bone marrow transplants.

How similar studies have performed: Previous studies have shown promise with cyclophosphamide in similar transplant settings, indicating potential for success.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Men and Women of Any Age
* Indication for an HSCT without matched sibling donor
* Have a matched unrelated donor (HLA 10 x 10 or 9 x 10)
* Hematological malignancy

Exclusion Criteria:

* Acute leukemias not in complete response (that is \> 5% blast in the bone marrow)
* Chemorefractory lymphoproliferative disease
* Active uncontrolled infection
* HCT-CI \> 3
* Severe organic disfunction (heart ejection fraction \< 45%, glomerular filtration rate \< 50 mL.hour, pulmonary DLCO \< 50%)
* Previous allogeneic bone marrow transplantation
* Contraindication to cyclophosphamide or ATG

Where this trial is running

São Paulo, São Paulo

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.

View on ClinicalTrials.gov →

Conditions: Bone Marrow Transplant Complications, Graft Versus Host Disease, Infection Viral, Engraft Failure, Immunologic Suppression, Bone Marrow Transplantation, Hematological Malignancies, Post-Cy

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.