Understanding the genetic causes of childhood liver cancer

Genetic and Molecular Basis of Pediatric Liver Cancer

Observational University of Pittsburgh · NCT03959800

This study is trying to find out the genetic causes of childhood liver cancer to help doctors diagnose and treat these rare cancers better.

Quick facts

Study typeObservational
Enrollment1600 (estimated)
Ages0 Years to 99 Years
SexAll
SponsorUniversity of Pittsburgh Academic / other
Locations1 site (Pittsburgh, Pennsylvania)
Trial IDNCT03959800 on ClinicalTrials.gov

What this trial studies

This observational study aims to explore the molecular and genetic basis of pediatric liver cancers, including hepatoblastoma and hepatocellular carcinoma. By collecting biological samples such as tumor tissue, saliva, and blood from affected patients and their families, the study seeks to improve classification systems based on tumor biology rather than just appearance. The goal is to identify genetic defects that could lead to better diagnoses and treatments for these rare cancers. The research will involve both retrospective and prospective data collection to achieve a comprehensive understanding of these conditions.

Who should consider this trial

Good fit: Ideal candidates include children under 21 years who have received treatment for a childhood liver tumor, as well as their biological parents and siblings.

Not a fit: Patients who have not received treatment for a childhood liver tumor or those with non-biological family members will not benefit from this study.

Why it matters

Potential benefit: If successful, this study could lead to more accurate diagnoses and effective treatments for childhood liver cancer.

How similar studies have performed: While pediatric liver cancers are rare, similar studies exploring genetic bases in other cancers have shown promise, indicating potential for success in this novel approach.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Prior or current treatment for a childhood liver tumor, malignant or benign, at age \<21 years.
* Biological parents and siblings of eligible children.

Exclusion Criteria:

* No prior or current treatment for a childhood liver tumor.
* Non-biological parents, legal guardians, or non-biological siblings of eligible children.

Where this trial is running

Pittsburgh, Pennsylvania

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Childhood Liver CancerLiver Malignant TumorsEmbryonal Sarcoma of LiverHepatoblastomaHepatocellular CarcinomaRhabdoid Tumor of LiverPediatric Liver Cancer
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.