Combining letrozole and simvastatin to treat hormone receptor positive breast cancer

A Randomized Window of Opportunity Study of Preoperative Letrozole and Simvastatin Versus Letrozole Alone in Stage I-III Hormone Receptor Positive, HER2 Negative Breast Cancer

Early Phase 1 Interventional Emory University · NCT05464810

This study tests if combining letrozole with simvastatin can help shrink tumors in postmenopausal women with hormone receptor positive breast cancer better than using letrozole alone.

Quick facts

PhaseEarly Phase 1
Study typeInterventional
Enrollment40 (estimated)
Ages18 Years and up
SexFemale
SponsorEmory University Academic / other
Drugs / interventionschemotherapy, immunotherapy
Locations4 sites (Atlanta, Georgia and 3 other locations)
Trial IDNCT05464810 on ClinicalTrials.gov

What this trial studies

This early phase I trial investigates the effectiveness of combining letrozole with simvastatin compared to letrozole alone in reducing tumor cell proliferation in postmenopausal women with stage I-III hormone receptor positive, HER2 negative breast cancer. The primary objective is to measure the decrease in Ki67, a biomarker for tumor growth, after 14 days of treatment. Secondary objectives include assessing immune activation changes and their correlation with tumor response, as well as evaluating safety and tolerability. The study aims to provide insights into the potential benefits of this combination therapy in a pre-surgical setting.

Who should consider this trial

Good fit: Ideal candidates are postmenopausal women aged 18 and older with biopsy-proven hormone receptor positive, HER2 negative stage I-III invasive breast cancer.

Not a fit: Patients with HER2 positive breast cancer or those who are not postmenopausal may not benefit from this study.

Why it matters

Potential benefit: If successful, this approach could enhance treatment efficacy for patients with hormone receptor positive breast cancer.

How similar studies have performed: While the combination of letrozole and simvastatin is a novel approach, similar studies have shown promise in enhancing cancer treatment outcomes.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Age \>= 18 years
* Biopsy proven hormone receptor positive, HER2 negative stage I-III invasive breast cancer

  * Estrogen receptor (ER) and/or progesterone receptor (PR) positivity are defined as \>= 10% of cells expressing hormonal receptors via IHC analysis
  * HER2 negativity is defined as either of the following by local laboratory assessment

    * IHC 0, 1+, or 2+ and in situ hybridization (ISH) non-amplified (ratio of HER2 to CEP17 \< 2.0 or single probe average HER2 gene copy number \< 4 signals/cell)
* Minimum primary tumor size 5 mm on any breast imaging (mammogram, ultrasound, magnetic resonance imaging \[MRI\])
* Baseline Ki-67 IHC expression on tumor tissue \>= 10%
* Post-menopausal women

  * Prior bilateral oophorectomy
  * Age \>= 55 years
  * Age \< 55 and amenorrheic for 12 months or more in the absence of chemotherapy, endocrine therapy, or ovarian suppression and follicle stimulating hormone (FSH), luteinizing hormone (LH), and estradiol in the postmenopausal range
* Eastern Cooperative Oncology Group (ECOG) performance status 0-2
* Prior treatment:

  * No systemic therapy (chemotherapy, immunotherapy, endocrine therapy, and/or investigational therapy) within 3 months of trial enrollment
* No statins, fibrates, or ezetimibe within 3 months of trial enrollment
* No active liver disease
* Hemoglobin \>= 9.0 g/dl (Note: the use of transfusion or other intervention to achieve hemoglobin \[Hgb\] \>= 9.0 g/dl is acceptable) (within 14 days prior to initiation of study treatment)
* Absolute neutrophil count (ANC) \>= 1,500/mcL (after at least 7 days without growth factor support or transfusion) (within 14 days prior to initiation of study treatment)
* Platelets \>= 100,000/mcL (within 14 days prior to initiation of study treatment)
* Total bilirubin =\< 2 institutional upper limit of normal (ULN) (within 14 days prior to initiation of study treatment)
* Aspartate aminotransferase (AST)/alanine aminotransferase (ALT) =\< 3 institutional ULN (within 14 days prior to initiation of study treatment)
* Serum creatinine =\< 2 mg/dL (or glomerular filtration rate \>= 40 mL/min) (within 14 days prior to initiation of study treatment)
* Willingness and ability of the subject to comply with scheduled visits, drug administration plan, protocol-specified laboratory tests, other study procedures, and study restrictions
* Be willing and able to provide written informed consent for the trial

Exclusion Criteria:

* Patients who are receiving any other investigational agents or an investigational device within 3 months before administration of first dose of study drugs
* History of allergic reactions attributed to compounds of similar chemical or biologic composition to simvastatin and/or letrozole
* Concomitant use of strong CYP3A4 inhibitors (i.e. clarithromycin, erythromycin, itraconazole, ketroconazole, nefazodone, Posaconazole, voriconazole, protease inhibitors \[including boceprevir and telaprevir\], telithromycin, cobicistat-containing products), cyclosporine, danazol, and gemfibrozil
* Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection, symptomatic congestive heart failure, unstable angina pectoris, cardiac arrhythmia, substance abuse disorders, or psychiatric illness/social situations that would limit compliance with study requirements
* Significant cardiovascular disease (e.g., myocardial infarction, arterial thromboembolism, cerebrovascular thromboembolism) within 3 months prior to start of study therapy; angina requiring therapy; symptomatic peripheral vascular disease; New York Heart Association class 3 or 4 congestive heart failure; or uncontrolled grade \>= 3 hypertension (diastolic blood pressure \>= 100 mmHg or systolic blood pressure \>= 160 mmHg) despite antihypertensive therapy
* Has a known additional malignancy that is progressing or requires active treatment. Exceptions include basal cell carcinoma of the skin or squamous cell carcinoma of the skin that has undergone potentially curative therapy

Where this trial is running

Atlanta, Georgia and 3 other locations

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Anatomic Stage I Breast Cancer AJCC v8Anatomic Stage II Breast Cancer AJCC v8Anatomic Stage III Breast Cancer AJCC v8HER2-Negative Breast CarcinomaHormone Receptor-Positive Breast CarcinomaInvasive Breast Carcinoma
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.