Combining decitabine with modified chemotherapy for high-risk acute leukemia before stem cell transplant

Decitabine Plus mBU/CY for High Risk Acute Leukemia With Minimal Residual Disease Pre-HSCT

Phase2; Phase3 Interventional Peking University People's Hospital · NCT03793517

This study is testing a new treatment combining decitabine and modified chemotherapy for people with high-risk acute leukemia to see if it helps them do better before getting a stem cell transplant.

Quick facts

PhasePhase2; Phase3
Study typeInterventional
Enrollment55 (estimated)
Ages18 Years to 55 Years
SexAll
SponsorPeking University People's Hospital Academic / other
Drugs / interventionscyclophosphamide
Locations1 site (Beijing, Beijing Municipality)
Trial IDNCT03793517 on ClinicalTrials.gov

What this trial studies

This clinical trial investigates the efficacy of a combination treatment involving decitabine and modified busulfan/cyclophosphamide (mBU/CY) as a preparative regimen for allogeneic hematopoietic stem cell transplantation (allo-HSCT) in patients with high-risk acute leukemia who have detectable minimal residual disease (MRD) prior to transplantation. Patients will receive decitabine followed by a specific chemotherapy regimen tailored for both HLA-mismatched and matched sibling transplantations. The study aims to monitor the patients' bone marrow samples at various time points post-transplant to assess leukemia status and potential relapse. This approach seeks to improve outcomes for patients at high risk of leukemia relapse after transplantation.

Who should consider this trial

Good fit: Ideal candidates for this study are patients with high-risk acute leukemia and detectable minimal residual disease prior to stem cell transplantation.

Not a fit: Patients who are pregnant or have uncontrolled severe infections may not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could significantly reduce the risk of leukemia relapse in high-risk patients undergoing stem cell transplantation.

How similar studies have performed: Previous studies have shown that decitabine can be effective in treating recurrent or refractory leukemia, suggesting potential success for this novel combination approach.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* acute leukemia patients with MLL-r,TLS-ERG,or SIL-TAL1,whose minimal residual disease were detectable pre-HSCT

Exclusion Criteria:

* pregnancy women
* uncontrolled severe infection

Where this trial is running

Beijing, Beijing Municipality

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Stem Cell Transplant ComplicationsLeukemia, Myeloid, AcuteLeukemia Relapsehigh risk acute myeloid leukemiahematopoietic stem cell transplantationleukemia relapsepreparation regimendecitabine
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.