Pilot-Feasibility Pilot for Batten Disease Translational Research
Official title: Pilot-Feasibility
Funded at Hugo W. Moser Res Inst Kennedy Krieger · NIH-11417537 · Data updated 2026-11-12
A small, dedicated funding core will support early, practicalBattten disease projects to speed up diagnosis, care, and potential treatments for children affected by Batten disease.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Hugo W. Moser Res Inst Kennedy Krieger NIH-funded |
| Lab location | 1 site (Baltimore, United States) |
| Project start | September 15, 2025 |
| Project end | August 31, 2030 |
| Funding year | 2026 |
| Award (this year) | $116,149 |
| NIH project number | 5U54HD122210-02 |
| Project ID | NIH-11417537 on NIH RePORTER |
Who could benefit from this research
✓Could help
Ideal candidates include pediatric patients with Batten disease or their families, and researchers with proposed translational or clinical pilot studies relevant to Batten disease.
✕Less likely to help
Patients not directly connected to Batten disease or without eligible pilot projects may not experience direct benefit.
What this research studies
This grant funds a Pilot Study Core within the Batten Disease Clinical Research Consortium to identify and fund short, high-potential translational and clinical pilot studies. The program emphasizes a patient-centric approach, collaboration across stakeholders, and a rigorous NIH-style review to select projects aligned with community priorities. By supporting early-stage ideas from both new and established researchers, the core aims to build clinical trial readiness and address critical needs in Batten disease care. Results could pave the way for larger studies and improved management for children and families affected by Batten disease.
Why it matters
Potential benefit: If successful, this core could accelerate new diagnostic tools, treatments, and better care strategies for Batten disease patients.
How similar studies have gone: The pilot-study approach has been used in other rare diseases to rapidly advance promising ideas toward clinical testing.
Where this research is happening
-
Hugo W. Moser Res Inst Kennedy Krieger
Baltimore, United States Active
Researchers
- Principal investigator: Thio, Kwee Liu Lin — Hugo W. Moser Res Inst Kennedy Krieger
- Study coordinator: Thio, Kwee Liu Lin
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About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page.