Pediatric Bone Marrow Failure Network: Pilot & Feasibility Governance Core
Official title: Pediatric Bone Marrow Failure Network (pBMFN) - Pilot & Feasibility Core
Funded at Boston Children's Hospital · NIH-11453339 · Data updated 2026-11-12
A program at Boston Children’s Hospital funds and mentors early-career researchers to pilot promising studies about pediatric bone marrow failure and to connect researchers with patients and families.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Boston Children's Hospital NIH-funded |
| Lab location | 1 site (Boston, United States) |
| Project start | August 21, 2026 |
| Project end | June 30, 2031 |
| Funding year | 2026 |
| Award (this year) | $126,529 |
| NIH project number | 1U54HD123051-01 |
| Project ID | NIH-11453339 on NIH RePORTER |
Who could benefit from this research
✓Could help
Candidates are children and adolescents affected by bone marrow failure and their families, plus early-career investigators pursuing pediatric BMF research.
✕Less likely to help
Patients not currently seeking research participation in pilot projects or those outside the pediatric BMF spectrum may not directly benefit.
What this research studies
This grant funds a governance core that creates processes to solicit, review, and fund pilot studies in pediatric bone marrow failure. It emphasizes developing the investigator pipeline, mentorship, and career growth while engaging patient families to align research with their priorities. The core also aims to build clinical trial readiness and foster collaboration among clinicians, scientists, and patient advocacy groups. Pilot projects will leverage the network’s infrastructure to advance diagnosis, treatment, and outcomes for children with BMF.
Why it matters
Potential benefit: If successful, it could accelerate new diagnostic tools and treatments for children with bone marrow failure.
How similar studies have gone: This approach has shown promise in other disease-focused networks by accelerating pilot studies and investigator development.
Where this research is happening
-
Boston Children's Hospital
Boston, United States Active
Researchers
- Principal investigator: Corey, Seth Joel — Boston Children's Hospital
- Study coordinator: Corey, Seth Joel
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About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page.