Pediatric Bone Marrow Failure Network Administrative Core
Official title: Pediatric Bone Marrow Failure Network (pBMFN) - Admin Core
Funded at Boston Children's Hospital · NIH-11453338 · Data updated 2026-11-12
A network-wide administrative core supports coordinated care, research, and future clinical trials for children with bone marrow failure.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Boston Children's Hospital NIH-funded |
| Lab location | 1 site (Boston, United States) |
| Project start | August 21, 2026 |
| Project end | June 30, 2031 |
| Funding year | 2026 |
| Award (this year) | $496,921 |
| NIH project number | 1U54HD123051-01 |
| Project ID | NIH-11453338 on NIH RePORTER |
Who could benefit from this research
✓Could help
Not a direct patient enrollment grant; supports infrastructure that could enable patient-centered research and trials for children with bone marrow failure.
✕Less likely to help
This core does not enroll patients itself and may have limited direct benefit to individual patients.
What this research studies
This grant funds the central administration for a national network of pediatric bone marrow failure programs, linking patient advocacy groups, clinical sites, and data resources. It focuses on organizing policies, fund use, communications, and biostatistical/data informatics support to ensure high-quality, collaborative research. The goal is to speed up access to optimized care and the readiness of sites to enroll children in future trials. Located at Boston Children’s Hospital, it coordinates multiple projects, cores, and partnerships to support families and clinicians.
Why it matters
Potential benefit: If successful, it could streamline care and trial readiness for children with bone marrow failure, potentially accelerating new treatments.
How similar studies have gone: Administrative cores like this have proven essential in coordinating multicenter pediatric rare-disease research and often lead to faster trial readiness.
Where this research is happening
-
Boston Children's Hospital
Boston, United States Active
Researchers
- Principal investigator: Shimamura, Akiko — Boston Children's Hospital
- Study coordinator: Shimamura, Akiko
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About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page.