Leukodystrophy Clinical Careers and Mentorship Network
Official title: Global Leukodystrophy Initiative Clinical Trials Network (GLIA- CTN)
Funded at Children's Hosp of Philadelphia · NIH-11599488 · Data updated 2026-11-12
A program to train, mentor, and support clinicians and researchers to advance care for people with leukodystrophies.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Children's Hosp of Philadelphia NIH-funded |
| Lab location | 1 site (Philadelphia, United States) |
| Project start | September 30, 2019 |
| Project end | August 31, 2027 |
| Funding year | 2026 |
| Award (this year) | $245,671 |
| NIH project number | 3U54NS115052-07S1 |
| Project ID | NIH-11599488 on NIH RePORTER |
Who could benefit from this research
✓Could help
Early-career clinicians and researchers who are interested in leukodystrophy research and who aim to contribute to patient care and translational work.
✕Less likely to help
This grant does not enroll patients directly and may not provide immediate treatment options.
What this research studies
This grant helps build a strong pipeline of clinicians and scientists focused on leukodystrophies by funding formal mentorship, predoctoral preparation, and translational career development. It supports parallel training pathways, including predoctoral programs, two leukodystrophy fellowships, and early-career development awards, with a focus on retention in rare-disease clinical research. The initiative also includes a leukodystrophy–specific communication training component to improve patient-family engagement and care planning. The goal is to sustain long-term clinical and translational progress for affected patients through targeted workforce development.
Why it matters
Potential benefit: Patients with leukodystrophies could benefit from a more experienced and dedicated workforce delivering better care and advancing treatments.
How similar studies have gone: Other rare-disease training and mentorship programs have improved retention of researchers and clinicians in the field, though this is a dedicated network for leukodystrophies.
Where this research is happening
-
Children's Hosp of Philadelphia
Philadelphia, United States Active
Researchers
- Principal investigator: Vanderver, Adeline Lucie — Children's Hosp of Philadelphia
- Study coordinator: Vanderver, Adeline Lucie
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About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page.