Condition
Usher Syndrome clinical trials and research
As of November 12, 2026, Find a Trial lists 5 Usher Syndrome clinical trials that are recruiting, at sites in 3 countries (most in United States (3), France (1), Germany (1)). By phase: Phase 1/2 (1), Phase 3 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 5Clinical trials
- 3Countries
Newest Usher Syndrome clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| NPI-001 for preserving photoreceptors in RP with Usher syndrome | Phase 3 | Dallas, Texas | Recruiting | Jul 17, 2026 |
| Short-term effects of transcorneal electrical stimulation on visual performance | — | Frankfurt am Main | Recruiting | Apr 23, 2026 |
| Natural history of vision loss in USH1B (MYO7A) and validation of virtual-reality vision tests | — | Paris, Île-de-France Region | Recruiting | Dec 12, 2025 |
| Investigating OpCT-001 for treating primary photoreceptor disease | Phase 1/2 | Los Angeles, California and 4 other locations | Recruiting | Jan 23, 2025 |
| Registry for inherited retinal degenerative diseases | — | Columbia, Maryland | Recruiting | May 6, 2015 |
All recruiting trials (5)
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NPI-001 for preserving photoreceptors in RP with Usher syndrome
This trial tests whether NPI-001 can slow vision loss in adults with RP linked to Usher syndrome, compared with a placebo over 24 months.
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Short-term effects of transcorneal electrical stimulation on visual performance
This study will see if a 30-minute session of transcorneal electrical stimulation with the OkuStim device produces short-term vision improvements in adults with retinitis pigmentosa or similar retinal degenerations who already use the device.
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Natural history of vision loss in USH1B (MYO7A) and validation of virtual-reality vision tests
This project tests how vision changes over time in people with USH1B caused by MYO7A mutations and whether virtual-reality mobility and visual-search tasks plus questionnaires can measure those changes.
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Investigating OpCT-001 for treating primary photoreceptor disease
This study is testing a new treatment called OpCT-001 to see if it can safely help adults with primary photoreceptor diseases, like Retinitis Pigmentosa and Usher Syndrome, improve their vision.
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Registry for inherited retinal degenerative diseases
This study is creating a registry for people with rare inherited eye diseases to help track their health and experiences over time, making it easier to understand these conditions and support research.
Related topics
Quick answers
How many Usher Syndrome clinical trials are recruiting right now?
5, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 3 countries. The most sites are in United States (3 trials), France (1 trial), Germany (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1/2: 1, Phase 3: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.