Condition
Congenital Myotonic Dystrophy clinical trials and research
As of November 12, 2026, Find a Trial lists 5 Congenital Myotonic Dystrophy clinical trials that are recruiting, at sites in 6 countries (most in United States (5), Italy (1), Brazil (1)). By phase: Phase 2/3 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 5Clinical trials
- 6Countries
Newest Congenital Myotonic Dystrophy clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| Assessing Readiness and Endpoints for Pediatric Myotonic Dystrophy | — | Little Rock, Arkansas and 3 other locations | Recruiting | Dec 24, 2024 |
| Assessing clinical endpoints in children with myotonic dystrophy | — | Los Angeles, California and 4 other locations | Recruiting | Feb 4, 2022 |
| Evaluating Tideglusib for Congenital Myotonic Dystrophy | Phase 2/3 | Little Rock, Arkansas and 13 other locations | Recruiting | Aug 13, 2021 |
| Online registry for myotonic dystrophy patients | — | Oakland, California | Recruiting | Mar 26, 2015 |
| Registry for Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy | — | Rochester, New York | Recruiting | Apr 30, 2004 |
All recruiting trials (5)
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Assessing Readiness and Endpoints for Pediatric Myotonic Dystrophy
This study is trying to improve how we understand and measure the effects of congenital and childhood myotonic dystrophy to help create better treatments for kids with these conditions.
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Assessing clinical endpoints in children with myotonic dystrophy
This study is trying to find better ways to measure how children with myotonic dystrophy are developing and feeling, so we can understand their condition and improve their care.
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Evaluating Tideglusib for Congenital Myotonic Dystrophy
This study is testing a new medication called tideglusib to see if it can help children and teenagers with Congenital Myotonic Dystrophy feel better over a year of treatment.
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Online registry for myotonic dystrophy patients
This study is creating an online registry for people with myotonic dystrophy to share their experiences and help researchers find better treatments.
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Registry for Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy
This study is creating a registry for people with myotonic dystrophy or facioscapulohumeral muscular dystrophy to share their health information and connect with researchers working to learn more about these conditions.
Related topics
Quick answers
How many Congenital Myotonic Dystrophy clinical trials are recruiting right now?
5, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 6 countries. The most sites are in United States (5 trials), Italy (1 trial), Brazil (1 trial), Australia (1 trial), Canada (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 2/3: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.