Using Pemigatinib for Advanced Gastrointestinal Cancer with FGFR Alterations

A Single-Arm Phase II Clinical Study of Pemigatinib in the Treatment of Advanced Gastrointestinal Cancer With FGFR 1-3 Alterations That Failed Standard Therapy

Phase 2 Interventional Tianjin Medical University Cancer Institute and Hospital · NCT05651672

This study is testing if a drug called Pemigatinib can help people with advanced gastrointestinal cancer that has certain genetic changes and hasn't worked with other treatments.

Quick facts

PhasePhase 2
Study typeInterventional
Enrollment100 (estimated)
Ages18 Years and up
SexAll
SponsorTianjin Medical University Cancer Institute and Hospital Academic / other
Drugs / interventionsanlotinib, lenvatinib, apatinib, pemigatinib
Locations1 site (Tianjin, Tianjin Municipality)
Trial IDNCT05651672 on ClinicalTrials.gov

What this trial studies

This phase II clinical trial evaluates the efficacy and safety of Pemigatinib in patients with advanced gastrointestinal cancer that has FGFR 1-3 alterations and has not responded to standard therapies. The study is designed as a single-arm trial, meaning all participants will receive the same treatment without a control group. Eligible patients must have measurable lesions and meet specific criteria related to their cancer and overall health. The goal is to determine how well Pemigatinib works in this specific patient population.

Who should consider this trial

Good fit: Ideal candidates are adults aged 18 or older with unresectable advanced gastrointestinal cancer and confirmed FGFR 1-3 alterations.

Not a fit: Patients with other malignant tumors or those who have previously used FGFR-targeting small molecule inhibitors may not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could provide a new therapeutic option for patients with advanced gastrointestinal cancer who have limited treatment choices.

How similar studies have performed: While this approach is focused on a specific genetic alteration in gastrointestinal cancer, similar studies targeting FGFR pathways have shown promise in other cancer types.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Aged 18 or older
* Histologically or cytologically confirmed unresectable advanced, recurrent or metastatic gastrointestinal cancer
* Have at least one measurable lesion according to RECIST v1.1
* With histologically confirmed FGFR1-3 alterations, including but not limited to amplification, mutation, fusion/rearrangement
* Disease progression after prior standard therapy
* No previous use of small molecule multi-target inhibitors targeting the FGFR pathway (including but not limited to anlotinib, lenvatinib, sorafenib, apatinib)
* ECOG performance status of 0\~1
* Expected survival time \> 3 months
* Sufficient organ functions
* Negative pregnancy test results of childbearing age women
* Patients at risk of conception (including their partners) need to use contraception

Exclusion Criteria:

* Diagnosed with malignant tumors other than gastrointestinal cancer within 5 years before the first dose, excluding radically cured cutaneous basal cell carcinoma, cutaneous squamous cell carcinoma, and/or radically resected carcinoma in situ
* Prior receipt of selective FGFR inhibitors
* Have received any other investigational drug or participated in another interventional clinical trial within 28 days before the first dose, or have received anti-tumor drug treatment within 28 days before the first dose (including Chinese herbal medicine with anti-tumor indications)
* Have not recovered ( ≤ grade 1 or reaching the baseline, excluding asthenia and alopecia) from toxicity and/or complications caused by any intervention before the start of treatment
* Known symptomatic central nervous system metastasis and/or carcinomatous meningitis.
* Known history of allotransplantation or allogeneic hematopoietic stem cell transplantation
* Abnormal laboratory parameters listed below:

  * Serum phosphate \> upper limit of normal (ULN)
  * Serum calcium exceeds the normal range, or the calcium concentration corrected for serum albumin exceeds the normal range when serum albumin exceeds the normal range
  * Potassium level \< lower limit of normal (LLN)#potassium levels can be corrected by supplements at screening
* Known history of human immunodeficiency virus (HIV) infection or confirmed with positive immune test results
* Presence of severe infection in the active phase or with poor clinical control
* Pleural effusion, ascites, or pericardial effusion with obvious clinical symptoms that require drainage
* Acute or chronic active hepatitis B or C infection
* Clinically significant or uncontrolled heart diseases, including unstable angina, acute myocardial infarction within 6 months before the first dose, grade III/IV congestive heart failure (New York Heart Association), and uncontrolled arrhythmia (patients with pacemakers or with atrial fibrillation but well controlled heart rate are allowed)
* ECG changes or medical history considered clinically significant by the investigator, QTcF interval \> 480 ms at screening, JTc interval can be used instead of QTc interval (in such cases, JTc must be ≤ 340 ms) for patients with intraventricular conduction block (QRS interval \> 120 ms)
* Uncontrolled hypertension (systolic pressure \> 160 mmHg or diastolic pressure \> 100 mmHg) after the optimal medical treatment, or a history of hypertensive crisis or hypertensive encephalopathy
* Hepatic encephalopathy, hepatorenal syndrome, or liver cirrhosis with Child-Pugh grade B or C
* Have received a major surgery (craniotomy, thoracotomy, or laparotomy) within 4 weeks prior to the first dose, or will receive a major surgery during the study treatment period
* Not fully recovered from toxicity and/or complications of a major surgery before the study treatment
* Pregnant or lactating women, or patients expected to conceive or give birth during the study period from the screening to the completion of the safety follow-up visit (90 days after the last dose for male subjects)
* Have received radiotherapy within 4 weeks before the first dose.
* History of disorders of calcium and phosphorus metabolism or systemic electrolyte metabolism imbalance with ectopic calcification of soft tissues (excluding calcification of soft tissues such as skin, kidneys, tendon, or blood vessels without systemic electrolyte metabolism imbalance caused by injury, disease, and old age)
* Clinically significant corneal or retinal diseases confirmed by ophthalmological examination
* Prior receipt of any potent CYP3A4 inhibitor or inducer within 14 days or 5 half lives (whichever is shorter) before the first dose. Ketoconazole is allowed for external use
* Known allergic reactions to pemigatinib or excipients of pemigatinib
* Unable or unwilling to swallow pemigatinib or are suffering from significant digestive system diseases that may interfere with absorption, metabolism, or excretion

Where this trial is running

Tianjin, Tianjin Municipality

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Gastrointestinal CancerPemigatinib
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.