Using advanced proton therapy to treat pediatric ependymoma

Pilot Trial of LET Optimized IMPT for Pediatric Patients With Ependymoma

Phase 1 Interventional M.D. Anderson Cancer Center · NCT03750513

This study is testing a new type of proton therapy for children with ependymoma to see if it safely targets tumors while protecting healthy tissue and improving their outcomes.

Quick facts

PhasePhase 1
Study typeInterventional
Enrollment48 (estimated)
AgesN/A to 22 Years
SexAll
SponsorM.D. Anderson Cancer Center Academic / other
Drugs / interventionschemotherapy, radiation
Locations2 sites (Boston, Massachusetts and 1 other locations)
Trial IDNCT03750513 on ClinicalTrials.gov

What this trial studies

This phase I trial investigates the safety and effectiveness of linear energy transfer (LET) optimized image modulated proton therapy (IMPT) in pediatric patients diagnosed with ependymoma. The study aims to evaluate the side effects of this innovative radiation therapy, which utilizes proton beams to target tumor cells while minimizing damage to surrounding healthy tissues. Additionally, advanced imaging techniques will be employed to identify biomarkers that reflect changes in the tumor and assess the treatment's impact on patient outcomes. Patients will receive treatment over a period of up to six weeks, followed by regular follow-ups to monitor their progress.

Who should consider this trial

Good fit: Ideal candidates include pediatric patients with confirmed ependymoma confined to the brain and who meet specific health criteria.

Not a fit: Patients with disseminated ependymoma or those who have previously received radiation therapy to the brain may not benefit from this study.

Why it matters

Potential benefit: If successful, this approach could lead to improved treatment outcomes and reduced side effects for children with ependymoma.

How similar studies have performed: While this approach is innovative, similar studies using advanced proton therapy techniques have shown promise in treating various cancers, suggesting potential for success.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Previous pathologic confirmation of ependymoma, World Health Organization (WHO) grade II or III
* Disease must be confined to the brain (no evidence of spread on MR imaging of the spine or on staging lumbar puncture)
* Patient may not receive chemotherapy concurrent with radiation
* Signed informed consent by patient and/or parents or legal guardian
* Lansky performance status score of 50 -100

Exclusion Criteria:

* Patients with previous radiation therapy to the brain
* Ependymoma of the spine
* Disseminated ependymoma requiring craniospinal radiation therapy
* Pregnancy
* Inability to undergo MR imaging
* Inability to receive gadolinium-based contrast agent

Where this trial is running

Boston, Massachusetts and 1 other locations

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Anaplastic EpendymomaEpendymoma
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.