Treatment for elderly patients with higher-risk myelodysplastic syndromes

Venetoclax Plus Azacytidine Conditioning Regimen Allo-HSCT for Elderly Patients With Higher-risk Myelodysplastic Syndromes

Phase1; Phase2 Interventional Navy General Hospital, Beijing · NCT06471946

This study is testing a new treatment combining two medications followed by a stem cell transplant to see if it helps older patients with higher-risk myelodysplastic syndromes live longer and have fewer complications.

Quick facts

PhasePhase1; Phase2
Study typeInterventional
Enrollment54 (estimated)
Ages70 Years and up
SexAll
SponsorNavy General Hospital, Beijing Academic / other
Locations1 site (Beijing, Beijing Municipality)
Trial IDNCT06471946 on ClinicalTrials.gov

What this trial studies

This phase 1/2 trial aims to evaluate the safety and efficacy of a conditioning regimen combining Venetoclax and Azacytidine followed by allogeneic hematopoietic stem cell transplantation (allo-HSCT) in elderly patients diagnosed with higher-risk myelodysplastic syndromes (MDS). The study will assess overall survival, progression-free survival, and the incidence of complications such as graft-versus-host disease over a two-year period post-transplantation. The trial will include patients who meet specific clinical criteria and are willing to adhere to the study protocol.

Who should consider this trial

Good fit: Ideal candidates for this study are elderly patients diagnosed with higher-risk myelodysplastic syndromes who can meet the trial's clinical requirements.

Not a fit: Patients with active or uncontrolled infections or significant systemic disease may not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could significantly improve survival rates and quality of life for elderly patients with higher-risk MDS.

How similar studies have performed: While there have been studies on similar treatments, this specific combination and approach in elderly higher-risk MDS patients is relatively novel.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* The patient should, in the investigator's opinion, be able to meet all clinical trial requirements.
* The patient is willing and able to adhere to the study visit schedule and other protocol requirements.
* The patient should be diagnosed with higher risk MDS according to the standard criteria of the World Health Organization (WHO).

Exclusion Criteria:

* Active or uncontrolled infections requiring systemic treatment within 14 days before enrollment.
* Any instability of systemic disease, including but not limited to severe cardiac, liver, kidney, or metabolic disease need therapy.

Where this trial is running

Beijing, Beijing Municipality

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Higher-risk Myelodysplastic Syndromes
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.