Treatment for adrenal insufficiency in patients with Cushing syndrome using osilodrostat

A Block-and-Replace Therapy With Osilodrostat and Concomitant Glucocorticoid Replacement

University of Michigan · NCT06430528

This study is testing if the medication osilodrostat, combined with a specific dose of another steroid, can help people with Cushing syndrome avoid adrenal insufficiency while keeping their hormone levels balanced.

Quick facts

Study typeObservational
Enrollment12 (estimated)
Ages18 Years to 75 Years
SexAll
SponsorUniversity of Michigan (other)
Locations1 site (Ann Arbor, Michigan)
Trial IDNCT06430528 on ClinicalTrials.gov

What this trial studies

This study aims to assess the incidence of adrenal insufficiency in patients with endogenous Cushing syndrome who are treated with osilodrostat alongside glucocorticoid replacement therapy. Participants will receive osilodrostat and a physiologic dose of methylprednisolone, with close monitoring and adjustments to medication based on cortisol levels. The study will also evaluate new biomarker steroids to ensure proper dosing and assess the safety and clinical outcomes of the treatment approach.

Who should consider this trial

Good fit: Ideal candidates include individuals diagnosed with endogenous Cushing syndrome who are either post-surgery or not candidates for surgery and are considering osilodrostat as part of their treatment.

Not a fit: Patients currently receiving other investigational drugs or those with hypersensitivity to osilodrostat may not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could improve the management of adrenal insufficiency in patients with Cushing syndrome, leading to better health outcomes.

How similar studies have performed: While this approach is novel in its specific combination of therapies, similar studies have shown promise in managing Cushing syndrome and adrenal insufficiency.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Endogenous Cushing syndrome, either following surgery or not candidates for surgery
* Under consideration to receive osilodrostat as part of their clinical care
* Able to provide informed consent.

Exclusion Criteria:

* Treatment with other investigational drugs within 30 days or five half-lives (whichever is longer).
* A history of hypersensitivity to osilodrostat or therapies of a similar chemical class.

Where this trial is running

Ann Arbor, Michigan

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.

View on ClinicalTrials.gov →

Conditions: Endogenous Cushing Syndrome, Adrenal Insufficiency, Hypercortisolism, Osilodrostat, Glucocorticoid, Methylprednisolone, Medrol

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.