Tracking awareness and management of familial hypercholesterolemia

CASCADE FH Registry (CAscade SCreening for Awareness and DEtection of Familial Hypercholesterolemia Registry)

The Familial Hypercholesterolemia Foundation · NCT01960244

This study is trying to see how well people with familial hypercholesterolemia are being treated and managed by tracking their health and experiences over time.

Quick facts

Study typeObservational
Enrollment5000 (estimated)
SexAll
SponsorThe Familial Hypercholesterolemia Foundation (other)
Locations1 site (Palo Alto, California)
Trial IDNCT01960244 on ClinicalTrials.gov

What this trial studies

The CASCADE-FH Registry is a national initiative designed to monitor therapy, clinical outcomes, and patient-reported outcomes for individuals with familial hypercholesterolemia (FH). This observational study involves collaboration among lipid specialists, cardiologists, primary care providers, and patients to enhance awareness and improve management of FH. Patients can enroll through clinics, an online portal, or via electronic health records, allowing for comprehensive data collection on their health status and treatment experiences. The registry aims to gather valuable insights that can lead to better outcomes for FH patients over time.

Who should consider this trial

Good fit: Ideal candidates include individuals with a clinical diagnosis of familial hypercholesterolemia or a genetic mutation associated with the condition.

Not a fit: Patients with hyperlipidemia due to other medical conditions, such as untreated hypothyroidism or nephrotic syndrome, may not benefit from this study.

Why it matters

Potential benefit: If successful, this initiative could significantly improve the management and outcomes of patients with familial hypercholesterolemia.

How similar studies have performed: Other studies focusing on familial hypercholesterolemia have shown promise in improving awareness and management, suggesting that this approach could be effective.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

Online Patient Enrollment Inclusion Criteria:

* Patients with existing clinical diagnosis of FH;
* Patients with genetic mutation of FH;
* Patients with an initial (pretreatment) LDL level \>190 mg/dL or total cholesterol \>300 mg/dL;
* Patients currently taking a lipid-lowering medication and have an LDL \>124 mg/dL or total cholesterol \>195 mg/dL.

Clinic Patient Enrollment Inclusion Criteria:

* Patients with existing clinical diagnosis of FH using one of the three clinical diagnostic (US MedPed Program Criteria, Simon Broome Register Criteria with diagnosis of "Probable", Dutch Lipid Clinic Network Diagnostic Criteria with diagnosis of "Probable")tools for FH; or
* Patients with genetic mutation of FH

Exclusion Criteria:

* Patients will be excluded from participation in the registry when a known medical condition other than FH that is thought to contribute to hyperlipidemia (i.e., untreated hypothyroidism, nephrotic syndrome, cholestasis hypopituitarism).

Where this trial is running

Palo Alto, California

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.

View on ClinicalTrials.gov →

Conditions: Hypercholesterolemia, familial, hypercholesterolemia, FH

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.