Investigating Tacrolimus Levels and Outcomes in Pediatric Stem Cell Transplant Patients

Factors Affecting the Tacrolimus Blood Concentration and Its Impact on Transplant-related Outcomes in Pediatric HSCT Recipients: a Single-center Retrospective Study

Observational University of Pisa · NCT06080490

This study looks at how the levels of a medication called tacrolimus in the blood affect the health outcomes of children who have received stem cell transplants.

Quick facts

Study typeObservational
Enrollment150 (estimated)
Ages1 Month to 18 Years
SexAll
SponsorUniversity of Pisa Academic / other
Drugs / interventionsmethotrexate
Locations1 site (Trieste)
Trial IDNCT06080490 on ClinicalTrials.gov

What this trial studies

This observational study aims to explore the relationship between tacrolimus blood concentrations and clinical outcomes in pediatric patients who have undergone allogeneic hematopoietic stem cell transplantation (HSCT). It will analyze various demographic and clinical factors that may influence tacrolimus levels and assess the incidence of graft-versus-host disease (GVHD) and transplant failure based on these levels. Data will be collected retrospectively from electronic medical records, ensuring adherence to Good Clinical Practice principles for accurate reporting and analysis.

Who should consider this trial

Good fit: Ideal candidates for this study are pediatric patients aged 0 to 18 years who are receiving tacrolimus for GVHD prophylaxis after allogeneic bone marrow transplantation.

Not a fit: Patients undergoing autologous bone marrow transplantation or those not receiving tacrolimus for GVHD prophylaxis may not benefit from this study.

Why it matters

Potential benefit: If successful, this study could enhance the understanding of tacrolimus dosing and its impact on transplant outcomes, potentially improving patient care in pediatric HSCT.

How similar studies have performed: Previous studies have shown varying success in understanding tacrolimus pharmacokinetics and its effects on transplant outcomes, making this investigation relevant and potentially impactful.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Age of the patients between 0 and 18 years (pediatric)
* Patients undergoing allogeneic bone marrow transplantation
* Patients' GVHD prophylaxis with tacrolimus
* Signed informed consent

Exclusion Criteria:

* Patients undergoing autologous bone marrow transplantation
* Patients not undergoing GVHD prophylaxis
* Patients undergoing cyclosporin prophylaxis
* Incomplete pharmacokinetic/pharmacodynamic data
* Lack of any informed consent

Where this trial is running

Trieste

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Graft Vs Host DiseaseTransplant FailureStem Cell Transplant ComplicationsHSCTTacrolimusGVHDPediatric patients
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.