International study on Chronic Myeloid Leukemia in children

INTERNATIONAL STUDY of Chronic Myeloid Leukaemia (CML) Treatment and Outcomes in Children and Adolescents

Observational Poitiers University Hospital · NCT01281735

This study looks at children and teens with Chronic Myeloid Leukemia to learn more about their treatment outcomes and side effects.

Quick facts

Study typeObservational
Enrollment750 (estimated)
AgesN/A to 18 Years
SexAll
SponsorPoitiers University Hospital Academic / other
Drugs / interventionsimatinib
Locations20 sites (North Adelaide, South Australia and 19 other locations)
Trial IDNCT01281735 on ClinicalTrials.gov

What this trial studies

This observational study aims to describe and characterize Chronic Myeloid Leukemia (CML) in a large cohort of pediatric patients. It focuses on children and adolescents diagnosed with Philadelphia positive and/or BCR-ABL positive CML, collecting data on treatment outcomes and side effects. The study is conducted internationally, involving multiple institutions to gather comprehensive epidemiological information that is currently lacking in this age group. By documenting the characteristics of CML in children, the study seeks to improve understanding and management of this rare disease.

Who should consider this trial

Good fit: Ideal candidates for this study are children and adolescents under 18 years of age diagnosed with Chronic Myeloid Leukemia.

Not a fit: Patients diagnosed with CML over the age of 18 will not benefit from this study.

Why it matters

Potential benefit: If successful, this study could enhance the understanding of CML in pediatric patients, leading to better treatment strategies and outcomes.

How similar studies have performed: While there have been limited studies on CML in children, this approach is novel in its comprehensive international data collection.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* patients less than 18 years of age
* diagnosed Philadelphia positive and/or BCR-ABL positive Chronic Myeloid Leukemia (CML) all phases

Exclusion Criteria:

* patients more than 18 years of age at diagnosis of CML

Where this trial is running

North Adelaide, South Australia and 19 other locations

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Chronic Myeloid Leukemiatreatment outcomeside effectsProtein Kinase Inhibitorspediatrics
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.