Evaluating the effects of exosomes in acute ischemic stroke

The Effect of Exosomes Derived From Human Induced Pluripotent Stem Cell (GD-iExo-003) in Acute Ischemic Stroke: an Exploratory Study.

Phase1; Phase2 Interventional Xuanwu Hospital, Beijing · NCT06138210

This study is testing if a new treatment using exosomes from stem cells can help people who have had an acute ischemic stroke feel better and recover safely.

Quick facts

PhasePhase1; Phase2
Study typeInterventional
Enrollment29 (estimated)
Ages18 Years to 70 Years
SexAll
SponsorXuanwu Hospital, Beijing Academic / other
Locations1 site (Beijing)
Trial IDNCT06138210 on ClinicalTrials.gov

What this trial studies

This multicenter, randomized, double-blinded, placebo-controlled, dose-escalation trial aims to assess the safety and preliminary efficacy of intravenous exosomes derived from human induced pluripotent stem cells (GD-iExo-003) in patients with acute ischemic stroke. The study consists of two parts: the first part involves a traditional 3+3 dose escalation design to determine the maximum tolerated dose, while the second part will randomize subjects to receive either the exosome treatment or a placebo. Participants will be monitored for dose-limiting toxicities and overall safety throughout the trial.

Who should consider this trial

Good fit: Ideal candidates are adults aged 18-70 with a clinical diagnosis of acute ischemic stroke and specific NIHSS scores.

Not a fit: Patients with severe comorbidities or those outside the specified age range may not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could provide a novel therapeutic option for improving outcomes in patients with acute ischemic stroke.

How similar studies have performed: While the use of exosomes in stroke treatment is a novel approach, similar studies have shown promise in other conditions, indicating potential for success.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Clinical diagnosis of acute ischemic stroke
* Age 18-70 years, inclusion of both genders
* Modified Rankin Scale score before stroke of 0-1
* NIHSS score 6-20 at inclusion that did not change by ≥4 points from screening to baseline assessment.
* Time of stroke onset is known and treatment can be started between day 1 and 7 of onset.
* Confirmation of hemispheric cortical infarct with magnetic resonance imaging or computed tomography
* Subjects who received intravenous thrombolysis or underwent mechanical reperfusion are eligible if they meet all other eligibility criteria.
* Adequate hepatic and renal function: serum aspartate aminotransferase ≤2.5× upper limit of normal; serum alanine aminotransferase ≤2.5× upper limit of normal; blood urea nitrogen ≤1.25× upper limit of normal; serum creatinine ≤1.25× upper limit of normal
* Adequate cardiac function.
* Subjects or legal representative can sign the informed consent and must be willing and able to comply with all aspects of treatment and follow-up schedule.

Exclusion Criteria:

* Presence of intracranial hemorrhage on CT including hemorrhagic stroke, epidural hematoma, subdural hematoma, intraventricular hemorrhage, intraventricular hemorrhage, subarachnoid hemorrhage or hemorrhagic transformation, etc.
* Presence of a lacunar or a brainstem infarct as the etiology of current symptoms.
* Evidence of brain tumor or history of epilepsy or traumatic brain injury.
* Subjects with present malignant disease.
* Subjects with severe comorbidities including immunodeficiency or coagulation disorders.
* Subjects with Alzheimer's disease, Parkinson's disease or other degenerative neurological disease.
* Ongoing systemic infection, severe local infection or taking immunosuppressants.
* Subjects with positive hepatitis B surface antibody (HBsAg) and positive hepatitis B core antibody (HBcAb), or HBsAg-positive virus carriers, positive hepatitis C antibody, positive syphilis antibody or HIV
* Allergy to the study products.
* Documented allergies
* Participation in any clinical trial in the last 3 months
* Inability or unwillingness to comply with the study schedule
* Pregnancy, childbearing potential (unless it is certain that pregnancy is not possible), oe breast feeding
* Other serious medical or psychiatric illness that is not adequately controlled
* Other circumstances that the investigator considers inappropriate for participation in the trial.

Where this trial is running

Beijing

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Acute Ischemic Strokeexosome
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.