Combining two drugs for treating aggressive meningiomas

Combination of Alpelisib and Trametinib in Progressive Refractory Meningiomas: Phase 1 Study

PHASE1 · Assistance Publique Hopitaux De Marseille · NCT03631953

This study is testing a combination of two drugs to see if they can help people with aggressive meningiomas that haven't improved with other treatments.

Quick facts

PhasePHASE1
Study typeInterventional
Enrollment25 (estimated)
Ages18 Years and up
SexAll
SponsorAssistance Publique Hopitaux De Marseille (other)
Drugs / interventionsTrametinib
Locations1 site (Marseille)
Trial IDNCT03631953 on ClinicalTrials.gov

What this trial studies

This clinical trial investigates the combination of Alpelisib, a PI3Kα inhibitor, and Trametinib, a MEK inhibitor, for patients with progressive refractory meningiomas that have not responded to previous treatments. The study aims to assess the safety and efficacy of this drug combination in inducing apoptosis in tumor cells and improving progression-free survival. Patients will undergo MRI scans to monitor tumor growth and will provide blood samples for analysis. The trial is designed for individuals who have exhausted other treatment options and have histologically confirmed meningiomas.

Who should consider this trial

Good fit: Ideal candidates include patients with grade I, II, or III meningiomas who have shown tumor progression after previous surgeries and radiotherapy.

Not a fit: Patients who are currently pregnant, breastfeeding, or have contraindications to Alpelisib and Trametinib will not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could significantly improve outcomes for patients with aggressive meningiomas that are resistant to current therapies.

How similar studies have performed: While the combination of these specific drugs in meningiomas is novel, similar approaches in other cancers have shown promising results.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Histologically proven meningioma grade I, II and III
* Progression is defined as growing meningiomas on 2 different Magnetic Resonance Imaging (MRI) 3 to 6 months apart
* Patients must have failed surgery, and not amenable to a new curative intended surgery
* Patients must have failed radiotherapy and/or radiosurgery
* Patients who have given their written consent
* No contra indication to Alpelisib and Trametinib
* No receiving other investigational agents
* Written informed consent
* Adequate bone marrow function
* Adequate liver function as shown by
* Adequate renal function

Exclusion Criteria:

* Contra indication to Alpelisib and Trametinib
* Women of child-bearing age who are using no effective means of contraception
* Pregnant or breast-feeding women
* Patients receiving other investigational agents
* Known intolerance or hypersensitivity to Alpelisib and Trametinib
* Uncontrolled diabetes mellitus
* Patients who have any severe and uncontrolled medical condition
* Patients receiving chronic treatment with immunosuppressives
* Patients with a known history of HIV seropositivity
* Patients who have a history of another primary malignancy less than or equal to 3 years, with
* the exceptions of non-melanoma skin cancer, and carcinoma in situ of uterine cervix

Where this trial is running

Marseille

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.

View on ClinicalTrials.gov →

Conditions: Meningioma

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.