Targeted nanoparticle therapy for drug-resistant glioblastoma

Tumor targeted drug delivery nanoplatform to overcome therapy resistance glioblastoma

['FUNDING_R01'] · MAYO CLINIC JACKSONVILLE · NIH-11248014

A tumor-targeted nanoparticle that delivers a new NRP1-blocking drug plus everolimus for people with glioblastoma that does not respond to standard treatment.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorMAYO CLINIC JACKSONVILLE (nih funded)
Locations1 site (JACKSONVILLE, UNITED STATES)
Trial IDNIH-11248014 on ClinicalTrials.gov

What this research studies

Researchers are developing a liposomal nanoparticle that carries a new, more soluble NRP1 inhibitor together with everolimus to reach glioblastoma cells and bypass the blood–brain barrier. The team is optimizing the drug formulation for stability and delivery so it can be stored and given reliably. Preclinical tests use patient-derived tumor cells and mouse models to check if the combination reduces therapy-resistant tumor-initiating cells and restores sensitivity to temozolomide. The long-term goal is to create a therapy that could be offered to people with recurrent, treatment-resistant GBM.

Who could benefit from this research

Good fit: People with recurrent or temozolomide-resistant glioblastoma, especially tumors showing NRP1-related biology, would be the most likely candidates.

Not a fit: Patients with non-glioblastoma brain tumors or whose disease is well controlled by standard treatments are unlikely to benefit from this work.

Why it matters

Potential benefit: If successful, this approach could make resistant glioblastoma more responsive to treatment and help extend patients' survival.

How similar studies have performed: Preclinical work showed that blocking NRP1 improved survival in mice and a first-generation liposomal combo helped resistant glioma cells, but this new, more soluble inhibitor and stable formulation are novel.

Where this research is happening

JACKSONVILLE, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: Brain Cancer

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.