NF1-linked glioblastoma

PROJECT 2: NF1-associated Glioblastoma

NIH-funded research Indiana University Indianapolis · NIH-11181020

This project looks for new therapy targets for people whose glioblastoma is driven by changes in the NF1 gene.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionIndiana University Indianapolis NIH-funded
Lab location1 site (Indianapolis, United States)
Project IDNIH-11181020 on NIH RePORTER

What this research studies

From a patient point of view, researchers are studying glioblastoma tumors that have NF1 gene changes to find specific weaknesses they can target. They use mouse models, patient-derived tumor grafts, lab-grown tumor cells, and real human tumor biopsies to compare tumors with germline versus somatic NF1 loss. The team also examines the tumor immune environment and tests candidate treatments first in preclinical models. Work is designed to translate findings toward therapies that could eventually be tested in patients.

Who could benefit from this research

Good fit: People with glioblastoma whose tumor tests positive for NF1 mutations or people with neurofibromatosis type 1 who develop glioblastoma.

Not a fit: Patients whose tumors do not have NF1 alterations or who have glioblastoma driven by different molecular changes are less likely to benefit directly from this project.

Why it matters

Potential benefit: If successful, this work could point to new targeted treatments or therapy strategies for patients with NF1-associated glioblastoma.

How similar studies have performed: Preclinical studies targeting NF1-driven tumors in other organs have shown promise, but effective therapies for NF1-linked glioblastoma in humans remain unproven.

Where this research is happening

Indianapolis, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Brain CancerCancer Suppressor GenesCancers
Last reviewed 2026-06-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.