Muscular Dystrophy Cell Line and Serum Banking Core
Funded at Research Inst Nationwide Children's Hosp · NIH-11397447 · Data updated 2026-11-12
A dedicated resource that creates and stores patient-derived muscle-related cell lines and blood samples to speed the development of genetic therapies for muscular dystrophy.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Research Inst Nationwide Children's Hosp NIH-funded |
| Lab location | 1 site (Columbus, United States) |
| Project start | August 15, 2024 |
| Project end | July 31, 2028 |
| Funding year | 2026 |
| Award (this year) | $305,035 |
| NIH project number | 5P50HD117373-03 |
| Project ID | NIH-11397447 on NIH RePORTER |
Who could benefit from this research
✓Could help
People with muscular dystrophy who consent to provide skin or blood samples for cell line and serum banking may participate indirectly through donation.
✕Less likely to help
Individuals not contributing samples or not affected by muscular dystrophy may not directly benefit from this resource.
What this research studies
This grant supports building and expanding a biobank of patient-derived muscle cells and related serum samples, using innovative methods to convert skin cells into muscle-like cells. Researchers will bank these cells and sera and improve techniques to produce usable myogenic cells, helping multiple muscular dystrophy projects study disease mechanisms and potential therapies. The core aims to streamline access to human material so scientists can test new genetic approaches more efficiently and safely before clinical trials.
Why it matters
Potential benefit: If successful, patients could benefit from faster translation of promising genetic therapies and more personalized research using their own cells and blood samples.
How similar studies have gone: Previous work funded by related grants has successfully created and banked hundreds of patient-derived cell lines and myogenic cells.
Where this research is happening
-
Research Inst Nationwide Children's Hosp
Columbus, United States Active
Researchers
- Principal investigator: Wein, Nicolas — Research Inst Nationwide Children's Hosp
- Study coordinator: Wein, Nicolas
Related research
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-
Endocrine role of intramuscular fat in muscular dystrophy
This grant studies how fat that builds up inside muscles in Duchenne and Becker muscular dystrophy may release hormones that affect overall health, especially metabolism.
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Stopping steroid-related muscle and bone wasting in Duchenne muscular dystrophy
Researchers are testing ways to protect muscles and bones in people with Duchenne muscular dystrophy who take long-term steroid medicines.
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Curation of muscular dystrophy genes to improve diagnosis and care
A grant to help doctors better interpret genetic tests for muscular dystrophy and myopathy so patients get clearer diagnoses and faster access to therapies.
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MR clues to how nNOS affects energy use and blood flow in Becker and Duchenne muscular dystrophy
This project looks at how advanced MRI tests can track muscle energy and blood flow changes in people with Becker and Duchenne muscular dystrophy as new gene therapies are explored.
About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page.