Investigating how specific brain cells contribute to abnormal movements in dystonia.

Cell Type Specific Genetic Manipulation to Dissect Cholinergic Interneuron Function and Plasticity in a Symptomatic Model of DYT1 Dystonia

NIH-funded research Ut Southwestern Medical Center · NIH-11017050

This study is looking at special brain cells that help control movement to understand why they don't work properly in people with DYT1 dystonia, a condition that causes twisting movements, and the goal is to find new ways to help those affected by similar movement issues.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUt Southwestern Medical Center NIH-funded
Lab location1 site (Dallas, United States)
Project IDNIH-11017050 on NIH RePORTER

What this research studies

This research focuses on cholinergic interneurons, which are important for controlling movement but are not well understood. The study aims to uncover how these neurons malfunction in conditions like DYT1 dystonia, a movement disorder. By using advanced genetic techniques in a mouse model, researchers will explore the cellular mechanisms that lead to abnormal twisting movements. The findings could help identify new treatment strategies for patients suffering from similar motor dysfunctions.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with DYT1 dystonia or those experiencing similar abnormal movements.

Not a fit: Patients with movement disorders not related to cholinergic dysfunction may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to improved treatments for patients with DYT1 dystonia and related movement disorders.

How similar studies have performed: Previous research has shown that targeting cholinergic neurons can lead to significant insights into movement disorders, suggesting this approach has potential for success.

Where this research is happening

Dallas, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Brain Diseases
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.