How a STAT1 gene change alters immune responses

Genomic regulation of immune response by a STAT1 gain of function mutation

NIH-funded research Ohio State University · NIH-11458029

This project looks at how a STAT1 gain-of-function genetic change rewires immune cells and contributes to infections and autoimmunity in people with STAT1-related disease.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionOhio State University NIH-funded
Lab location1 site (Columbus, UNITED STATES)
Project IDNIH-11458029 on NIH RePORTER

What this research studies

The team uses a mouse model carrying the same STAT1 mutation seen in patients to watch how immune cells respond to infections over time. They study long-lasting changes in gene control (epigenetics) after exposure to cytokines and map which genes and regulatory regions are altered. Experiments include looking at liver immune cells, the role of the microbiome, and genomic assays such as ATAC-seq, and the work is linked back to samples or data from affected people. The aim is to understand why people with STAT1-GOF have both fungal susceptibility and severe viral or inflammatory complications.

Who could benefit from this research

Good fit: People with confirmed STAT1 gain-of-function mutations, or patients with recurrent fungal and/or severe viral infections and related autoimmune symptoms, would be the most relevant candidates to contribute samples or be considered for future therapies.

Not a fit: People without STAT1 mutations or those with unrelated causes of immune problems are unlikely to directly benefit from the findings in the near term.

Why it matters

Potential benefit: If successful, this work could reveal why STAT1-GOF patients get specific infections and point to new targets or strategies to correct immune imbalances.

How similar studies have performed: Prior clinical and laboratory studies have shown that STAT1-GOF causes immune imbalances and infection risk, but using epigenetic mapping and microbiome-linked tissue studies to explain long-term reprogramming is a newer approach.

Where this research is happening

Columbus, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Autoimmune Diseases
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.