Condition
Urea Cycle Disorders, Inborn clinical trials and research
As of November 12, 2026, Find a Trial lists 2 Urea Cycle Disorders, Inborn clinical trials that are recruiting, at sites in 4 countries (most in Australia (1), France (1), United Kingdom (1)). By phase: Phase 1/2 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 2Clinical trials
- 4Countries
All recruiting trials (2)
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KRRO-121 for hyperammonemia in urea cycle disorders: a first-in-human study
This study tests KRRO-121, a treatment designed to help clear ammonia, in adults with urea cycle disorders and in healthy volunteers to see if it is safe and how it acts in the body.
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Long-term follow-up for participants in an iECURE protocol
This study looks at the long-term safety and effectiveness of a treatment for people who have already been part of an earlier study, while also tracking the health of those who didn’t receive the treatment.
Related topics
Quick answers
How many Urea Cycle Disorders, Inborn clinical trials are recruiting right now?
2, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 4 countries. The most sites are in Australia (1 trial), France (1 trial), United Kingdom (1 trial), United States (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1/2: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.