Condition

Progressive Familial Intrahepatic Cholestasis clinical trials and research

• 6Clinical trials
• 11Countries

Newest Progressive Familial Intrahepatic Cholestasis clinical trials

All recruiting trials (6)

• Odevixibat for PFIC in China: Real-world Safety and Effectiveness

  This registry collects real-world safety and effectiveness data on children with PFIC who are being treated with odevixibat in China.

  Recruiting at 2 sites Ipsen · Beijing and 5 other locations · NCT07588880

• Finding genetic causes of adult-onset cholestatic liver disease

  This study uses whole-genome sequencing to try to find rare genetic causes in adults with unexplained cholestatic liver disease so care can be better tailored.

  Recruiting Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico · Milan, Milano · NCT07317193

• Long-term safety and outcomes of Livmarli for Alagille syndrome in the EU

  This study will follow people with Alagille syndrome who take Livmarli to see if it is safe, well tolerated over the long term, and continues to reduce cholestatic itching.

  Recruiting at 13 sites Phase 4 Mirum Pharmaceuticals, Inc. · Brussels and 14 other locations · NCT07290257

• Long-term outcomes of odevixibat (Bylvay) for people with PFIC in South Korea

  This registry will see how well odevixibat controls symptoms and how safe it is over time for people with Progressive Familial Intrahepatic Cholestasis (PFIC) in South Korea.

  Recruiting at 2 sites Ipsen · Gyeongsang and 4 other locations · NCT07185919

• Observational analysis of Progressive Familial Intrahepatic Cholestasis treatment

  This study is looking at how different treatments for Progressive Familial Intrahepatic Cholestasis work and what happens to patients over time to help improve care for those with this rare liver disease.

  Recruiting University Medical Center Groningen · Groningen · NCT06778174

• Evaluating the long-term safety and outcomes of Livmarli in patients with liver diseases

  This study is testing how safe and effective the medication Livmarli is for people with Alagille syndrome or Progressive familial intrahepatic cholestasis over a five-year period.

  Recruiting at 8 sites Mirum Pharmaceuticals, Inc. · Los Angeles, California and 7 other locations · NCT06193928

Related topics

Quick answers

How many Progressive Familial Intrahepatic Cholestasis clinical trials are recruiting right now?

6, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.

Where are these trials running?

In 11 countries. The most sites are in Netherlands (2 trials), Italy (2 trials), China (1 trial), United States (1 trial), South Korea (1 trial). Each study page lists its sites and which ones are recruiting.

What phases are they in?

Phase 4: 1. Trials with no phase listed are usually device, behavioural or observational studies.

How do I join one?

Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.

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