Condition

MLD clinical trials and research

• 2Clinical trials
• 1Country

All recruiting trials (2)

• Long-term observation of rare genetic brain disorders

  This study is tracking how rare genetic brain disorders progress over time to better understand their effects on patients.

  Recruiting University of Pittsburgh · Pittsburgh, Pennsylvania · NCT03333200

• Collecting data and samples from patients with leukodystrophy

  This study is collecting health information and samples from people with leukodystrophy to help find new causes and better treatments for the condition.

  Recruiting at 23 sites Children's Hospital of Philadelphia · Los Angeles, California and 22 other locations · NCT03047369

Related topics

Quick answers

How many MLD clinical trials are recruiting right now?

2, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.

Where are these trials running?

All of them have sites in United States. Each study page lists its sites and which ones are recruiting.

How do I join one?

Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.

Find the studies that fit you

A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.

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