Condition

Gene Therapy clinical trials and research

• 6Clinical trials
• 3Countries

Newest Gene Therapy clinical trials

All recruiting trials (6)

• KLN-1010 gene therapy for relapsed or refractory multiple myeloma

  This Phase 1 trial will try KLN-1010, an in vivo CAR‑T gene therapy, to see if it is safe and can be given at a tolerable dose for people with relapsed or refractory multiple myeloma who have had at least three prior therapies.

  Recruiting at 11 sites Phase 1 Kelonia Therapeutics, Inc. · Duarte, California and 10 other locations · NCT07075185

• Perceptual evaluation and rehabilitation program for congenital hearing loss

  This project will try a gamified, age‑adjusted software program to measure and train speech, music, and spatial hearing in people born with hearing loss who use hearing aids, cochlear implants, or gene therapy.

  Recruiting Eye & ENT Hospital of Fudan University · Shanghai · NCT07024524

• Comparing growth and development in children with beta-thalassemia after gene therapy

  This study looks at how gene therapy affects the growth and development of children with beta-thalassemia compared to those getting regular treatments and healthy kids.

  Recruiting Institute of Hematology & Blood Diseases Hospital, China · Tianjin, Tianjin Municipality · NCT05991336

• Gene therapy for hemophilia A in adults

  This study is testing a new gene therapy to see if it can safely help adults with hemophilia A who have very low levels of a crucial clotting factor.

  Recruiting Institute of Hematology & Blood Diseases Hospital, China · Tianjin, Tianjin Municipality · NCT04728841

• Gene therapy for X-linked severe combined immunodeficiency using targeted busulfan conditioning

  This study is testing a new gene therapy for patients with X-linked severe combined immunodeficiency to see if it can help their immune system work better after a special treatment to prepare their bodies.

  Recruiting at 4 sites Phase 1/2 Boston Children's Hospital · Los Angeles, California and 3 other locations · NCT03311503

• Comprehensive database for studying stem cell transplants and cellular therapies

  This study is creating a database to gather information on stem cell transplants and treatments to help improve recovery for patients and donors and make these therapies more accessible to everyone.

  Recruiting at 2 sites Center for International Blood and Marrow Transplant Research · Minneapolis, Minnesota and 1 other locations · NCT01166009

Related topics

Quick answers

How many Gene Therapy clinical trials are recruiting right now?

6, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.

Where are these trials running?

In 3 countries. The most sites are in United States (3 trials), China (3 trials), Australia (1 trial). Each study page lists its sites and which ones are recruiting.

What phases are they in?

Phase 1: 1, Phase 1/2: 1. Trials with no phase listed are usually device, behavioural or observational studies.

How do I join one?

Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.

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