Condition

Duchene Muscular Dystrophy clinical trials and research

• 4Clinical trials
• 11Countries

Newest Duchene Muscular Dystrophy clinical trials

All recruiting trials (4)

• GNT0004 gene therapy for Duchenne muscular dystrophy in ambulant boys

  This study tests a one-time IV gene therapy (GNT0004) to see if it slows DMD progression in ambulant boys aged 6–10.

  Recruiting at 10 sites Phase 2/3 Genethon · Brussels and 13 other locations · NCT07856329

• AOC 1044 in Duchenne Muscular Dystrophy with Exon 44 Skipping

  This study tests whether intravenous AOC 1044 helps boys with Duchenne muscular dystrophy caused by mutations amenable to exon 44 skipping.

  Recruiting at 20 sites Phase 3 Avidity Biosciences, Inc. · Westmead, New South Wales and 19 other locations · NCT07587242

• Ultrafast ultrasound biomarkers to track Duchenne and Becker muscular dystrophy

  This study tests whether multiparametric ultrafast ultrasound can non-invasively monitor disease progression in people with Duchenne or Becker muscular dystrophy.

  Recruiting Nantes University Hospital · Nantes · NCT07378553

• Real-world experience of oral givinostat for Duchenne muscular dystrophy in the U.S.

  The study will track safety and functional outcomes in people aged 6 and older with Duchenne muscular dystrophy who start oral givinostat during routine U.S. care to see how the medicine is tolerated and how patients do over time.

  Recruiting at 9 sites ITF Therapeutics LLC · Little Rock, Arkansas and 8 other locations · NCT07127978

Related topics

Quick answers

How many Duchene Muscular Dystrophy clinical trials are recruiting right now?

4, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.

Where are these trials running?

In 11 countries. The most sites are in France (3 trials), Belgium (2 trials), Spain (2 trials), United Kingdom (2 trials), Australia (1 trial). Each study page lists its sites and which ones are recruiting.

What phases are they in?

Phase 3: 1, Phase 2/3: 1. Trials with no phase listed are usually device, behavioural or observational studies.

How do I join one?

Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.

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