Condition
Acid SphingoMyelinase Deficiency clinical trials and research
As of November 12, 2026, Find a Trial lists 2 Acid SphingoMyelinase Deficiency clinical trials that are recruiting, at sites in 2 countries (most in Spain (1), United States (1)). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 2Clinical trials
- 2Countries
All recruiting trials (2)
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Long-term safety and immune response of olipudase alfa in young children with acid sphingomyelinase deficiency
This study is testing the long-term safety and immune response of a treatment called olipudase alfa in young children under 2 years old who have acid sphingomyelinase deficiency.
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Prevalence of Acid Sphingomyelinase Deficiency and Gaucher Disease in Patients with Monoclonal Gammopathies
This study is trying to see how common Acid Sphingomyelinase Deficiency and Gaucher Disease are in patients with monoclonal gammopathies, especially those with an enlarged spleen or who have had their spleen removed.
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Quick answers
How many Acid SphingoMyelinase Deficiency clinical trials are recruiting right now?
2, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 2 countries. The most sites are in Spain (1 trial), United States (1 trial). Each study page lists its sites and which ones are recruiting.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.