Using high-dose oral montelukast to treat asthma exacerbations in children

Dose Escalation Clinical Trial of High-dose Oral Montelukast to Inform Future RCT in Children With Acute Asthma Exacerbations

PHASE2 · Vanderbilt University Medical Center · NCT05819541

This study is testing whether high doses of a medication called montelukast can help children aged 4 to 12 who are having serious asthma attacks feel better after using their inhalers.

Quick facts

PhasePHASE2
Study typeInterventional
Enrollment90 (estimated)
Ages4 Years to 12 Years
SexAll
SponsorVanderbilt University Medical Center (other)
Locations1 site (Nashville, Tennessee)
Trial IDNCT05819541 on ClinicalTrials.gov

What this trial studies

This clinical trial aims to determine the optimal dosage of high-dose oral montelukast for children aged 4 to 12 experiencing moderate to severe asthma exacerbations after initial treatment with inhaled albuterol. The study will utilize an adaptive, double-masked randomized controlled trial design, where participants will receive either montelukast or a placebo, with doses adjusted based on pharmacokinetic modeling. The primary goal is to achieve a peak plasma concentration of montelukast that is effective in reducing asthma symptoms, as measured by the Acute Asthma Intensity Research Score (AAIRS).

Who should consider this trial

Good fit: Ideal candidates are children aged 4 to 12 years with doctor-diagnosed asthma who present with moderate to severe exacerbations.

Not a fit: Patients with acute or chronic liver disease, allergies to montelukast, or significant neuropsychiatric disorders may not benefit from this study.

Why it matters

Potential benefit: If successful, this study could provide a more effective treatment option for children suffering from acute asthma exacerbations.

How similar studies have performed: Previous studies have shown that intravenous montelukast can rapidly improve lung function in adults, suggesting potential success for high-dose oral montelukast in children.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Child aged 4 - 12 years with doctor-diagnosed asthma
* Presents to the Vanderbilt Children's Hospital with an acute asthma exacerbation that is moderate or severe (AAIRS \>7) after initial treatment with inhaled albuterol
* The parent agrees to phone and/or mail follow-up at 2-3 weeks for completion of SCARED and side-effect questionnaires.

Exclusion Criteria:

* Gestational age \< 34 weeks
* acute or chronic liver disease
* allergy to montelukast
* female with any evidence of Tanner stage 2 or greater breast development
* gastroesophageal reflux requiring acid-blocking medication
* history of anxiety disorder, depression and/or other neuropsychiatric disorder except ADHD
* positive on question 1 or 2 of the Columbia Suicide Severity Rating Scale (CSSR-S)
* score \>25 on the 82-point Screen for Child Anxiety Related Disorders (SCARED) questionnaire
* Patients currently receiving daily montelukast (4 or 5 mg) will not be excluded from study participation.

Where this trial is running

Nashville, Tennessee

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.

View on ClinicalTrials.gov →

Conditions: Status Asthmaticus

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.