Using darbepoetin to help newborns recover from ischemic stroke

Darbepoetin for Ischemic Neonatal Stroke to Augment Regeneration

Phase 2 Interventional UMC Utrecht · NCT03171818

This study is testing if a medication called darbepoetin can help newborns recover better from a type of stroke by promoting brain healing.

Quick facts

PhasePhase 2
Study typeInterventional
Enrollment80 (estimated)
AgesN/A to 7 Days
SexAll
SponsorUMC Utrecht Academic / other
Locations1 site (Utrecht)
Trial IDNCT03171818 on ClinicalTrials.gov

What this trial studies

This study investigates the effects of darbepoetin, an erythropoiesis-stimulating agent, on newborns diagnosed with perinatal arterial ischemic stroke (PAIS) confirmed by MRI. It is a randomized, double-blind, placebo-controlled trial where infants will receive either darbepoetin or a saline placebo to assess its ability to promote neuronal tissue formation and restore brain function. The ultimate goal is to develop a therapy that can mitigate the long-term consequences of brain injury associated with PAIS in term newborns.

Who should consider this trial

Good fit: Ideal candidates are newborns aged 36 weeks or older with MRI-confirmed acute PAIS involving the middle cerebral artery.

Not a fit: Patients with severe hypoxic-ischemic encephalopathy or major congenital anomalies are unlikely to benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could significantly improve recovery outcomes for newborns affected by ischemic strokes.

How similar studies have performed: While the use of darbepoetin in this context is novel, previous studies on erythropoiesis-stimulating agents have shown promise in other neurological conditions.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Newborns ≥ 36+0 weeks of gestation, both male and female
* MRI confirmed diagnosis of acute PAIS, in the MCA region with involvement of the cortical spinal tract (e.g. Posterior Limb of Internal Capsule \[PLIC\] or peduncles) within one week after birth
* Written informed consent from custodial parent(s)

Exclusion Criteria:

* Moderate -severe Hypoxic-Ischemic Encephalopathy (HIE) with or without hypothermia therapy
* Any proven or suspected major congenital anomaly, chromosomal disorder, metabolic disorder;
* Presence of a serious infection of the central nervous system;
* No realistic prospect of survival, (e.g. severe brain injury), at the discretion of the attending physician.
* Infant for whom withdrawal of supportive care is being considered.

Where this trial is running

Utrecht

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions PAISNeonatal StrokePerinatal Stroke
Last reviewed 2026-06-09 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.