Using colchicine to treat intracranial atherosclerotic disease

Colchicine Use in Intracranial Atherosclerotic Disease - a Pilot Open-labelled Randomized Trial

Phase 2 Interventional Chinese University of Hong Kong · NCT05503225

This study is testing if a low dose of colchicine can help people who have had a recent stroke due to narrowed blood vessels in the brain feel better and avoid more serious health problems.

Quick facts

PhasePhase 2
Study typeInterventional
Enrollment72 (estimated)
Ages40 Years to 80 Years
SexAll
SponsorChinese University of Hong Kong Academic / other
Locations1 site (Hong Kong)
Trial IDNCT05503225 on ClinicalTrials.gov

What this trial studies

This pilot randomized, double-blind, placebo-controlled trial aims to evaluate the efficacy of low-dose colchicine in patients with recent ischemic stroke due to intracranial atherosclerosis (ICAD) with significant stenosis. A total of 44 patients will be recruited and randomly assigned to receive either colchicine or a placebo for 12 months. The primary endpoint will assess the regression of intracranial stenosis, plaque volume, and the occurrence of major adverse cardiovascular or cerebrovascular events. High-resolution magnetic resonance imaging will be utilized to monitor changes in plaque characteristics over the study period.

Who should consider this trial

Good fit: Ideal candidates are Chinese patients aged 40-80 years with symptomatic ICAD of ≥ 50% stenosis who have experienced a first-ever ischemic stroke within the last 8 weeks.

Not a fit: Patients who are unable to provide informed consent or have contraindications to colchicine therapy will not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could significantly reduce the risk of recurrent strokes in patients with ICAD.

How similar studies have performed: While colchicine has shown promise in reducing stroke incidence in high cardiovascular risk patients, this specific application in ICAD is novel and has not been extensively tested.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria

1. Chinese patients aged 40-80 years old
2. Patients with symptomatic ICAD of ≥ 50% stenosis in middle cerebral arteries, basilar artery. Degree of stenosis will be quantified by computer tomographic angiography (CTA), magnetic resonance imaging (MRI) or digital subtraction angiography (DSA) by the WASID method (13). Symptomatic ICAD is defined as ischemic stroke or transient ischemic attack with clinical or radiological signs correspond to the vascular territory supplied by the disease vessel.
3. Patients with first-ever ischaemic stroke within 8 weeks of recruitment

Exclusion Criteria

1. Patients who are unable to provide an informed consent
2. Patients who are contraindicated to contrast MRI scans, e.g. non-MRI compatible pacemaker, claustrophobia, known gadolinium-based contrast allergy, estimated glomerular filtration rate \< 30mL/min/1.73m2, etc.
3. Patients who have absolute or relative contraindications to colchicine therapy, e.g. colchicine allergy, neuromuscular disorders, haematological diseases, chronic diarrhea, estimated glomerular filtration rate \< 30mL/min/1.73m2, chronic liver disease, etc.
4. Patients with intracranial stenosis not due to atherosclerosis, e.g. vasculitis, vasospasm, Moyamoya disease, etc.
5. Pregnancy
6. Patients with elevated creatine kinase level at randomisation stage of study.
7. Recurrent gouty arthritis that requires colchicine for \> 3 months per year;
8. Inflammatory bowel disease or chronic diarrhea;
9. Neuromuscular disease or a nontransient creatine kinase level that was greater than three times the upper limit of the normal range (unless due to infarction) for \> 3 months;
10. Clinically significant nontransient hematologic abnormalities with hemoglobin \<10g/dL, white blood cell \< 4x10\^9, or platelet \< 100x10\^9/L for \> 3 months;
11. Alcoholism;
12. Long term systemic glucocorticoid therapy

Where this trial is running

Hong Kong

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions ICAD - Intracranial Atherosclerotic DiseaseICADCVAcolchicine
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.