Treatment of Chronic Myeloid Leukemia with ELVN-001 in Japanese Patients

A Phase 1 Study of ELVN-001 for the Treatment of Chronic Myeloid Leukemia With and Without T315I Mutation in Japanese Participants

Phase 1 Interventional Enliven Therapeutics · NCT06787144

This study is testing a new treatment called ELVN-001 for Japanese patients with chronic myeloid leukemia who haven't had success with other medications to see if it's safe and effective.

Quick facts

PhasePhase 1
Study typeInterventional
Enrollment21 (estimated)
Ages18 Years and up
SexAll
SponsorEnliven Therapeutics Industry-sponsored
Locations4 sites (Akita, Akita and 3 other locations)
Trial IDNCT06787144 on ClinicalTrials.gov

What this trial studies

This clinical trial evaluates the safety and tolerability of ELVN-001, a new treatment for chronic myeloid leukemia (CML), in Japanese patients who have not responded to or cannot tolerate at least two prior tyrosine kinase inhibitors (TKIs). It is a first-in-human, dose escalation study aimed at determining the recommended dose for further evaluation. The study will also assess the pharmacokinetics and anti-CML activity of ELVN-001, particularly in patients with or without the T315I mutation. The findings will inform future development of this treatment for adults with CML.

Who should consider this trial

Good fit: Ideal candidates are Japanese patients with chronic phase CML who have failed or are intolerant to at least two prior TKIs.

Not a fit: Patients currently receiving anti-cancer therapy or those with certain pancreatic conditions may not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could provide a new option for patients with chronic myeloid leukemia who have limited treatment alternatives.

How similar studies have performed: While this approach is novel, similar studies targeting CML have shown promise in developing new treatments.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* BCR::ABL1 positive CP-CML that has failed, or the patient is intolerant to, or not a candidate for, at least 2 prior TKIs.
* ECOG performance status of 0 to 2.
* The patient was born in Japan and both parents and grandparents are Japanese.
* Adequate hematologic, hepatic and renal function.
* Prior bone marrow transplant allowed if ≥ 6 months prior to the first dose of ELVN-001.

Exclusion Criteria:

* Treatment with anti-cancer or anti-CML therapy within 7 days or 5 half-lives, whichever is longer.
* History of acute tyrosine kinase inhibitor (TKI)-related pancreatitis within 6 months of study entry. Active chronic pancreatitis, or pancreatic disease due to any cause.
* QTc \>470 ms.

Where this trial is running

Akita, Akita and 3 other locations

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions CMLChronic Phase CMLTyrosine Kinase InhibitorT315IT315I MutantBCR-ABL
Last reviewed 2026-06-10 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.