Safety study of avalglucosidase alfa during pregnancy

A Descriptive Safety Study Based on Data Collected From Women and Their Offspring Exposed to Nexviazyme/Nexviadyme (Avalglucosidase Alfa-ngpt/Avalglucosidase Alfa) During Pregnancy and/or Lactation in the Postmarketing Setting

Observational Sanofi · NCT05734521

This study is looking at how safe the drug avalglucosidase alfa is for pregnant women and their babies during pregnancy and breastfeeding.

Quick facts

Study typeObservational
Enrollment100 (estimated)
SexFemale
SponsorSanofi Industry-sponsored
Locations1 site (Bridgewater, New Jersey)
Trial IDNCT05734521 on ClinicalTrials.gov

What this trial studies

This observational study aims to collect data on the safety of avalglucosidase alfa in women and their offspring during pregnancy and lactation. It will assess potential risks and complications associated with the drug for both mothers and their developing children. The study will follow participants for at least 10 years, evaluating outcomes in exposed infants, including their growth and development through the first year of life. Data will be gathered retrospectively and prospectively to provide a comprehensive understanding of the drug's effects.

Who should consider this trial

Good fit: Ideal candidates include women who have been exposed to avalglucosidase alfa during pregnancy or lactation and have consented to participate.

Not a fit: Patients who have not been exposed to avalglucosidase alfa during pregnancy or lactation may not benefit from this study.

Why it matters

Potential benefit: If successful, this study could provide critical safety information for pregnant women with Pompe disease using avalglucosidase alfa.

How similar studies have performed: While this study focuses on a specific population, similar observational studies have provided valuable safety data for other medications during pregnancy.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Women and their offspring exposed to avalglucosidase alfa during pregnancy and/or lactation for whom an Individual Case Safety Report (ICSR) has been submitted to the Sanofi Global Pharmacovigilance (PV) department, and/or,
* Women exposed to avalglucosidase alfa during pregnancy and/or lactation who have provided informed consent to enroll in the Pompe Pregnancy Sub-registry.

Exclusion Criteria:

There are no exclusion criteria in this study.

The above information is not intended to contain all considerations relevant to a potential participation in a clinical trial.

Where this trial is running

Bridgewater, New Jersey

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Pompe DiseasePregnancy
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.