Nicotinamide riboside supplementation to improve stem cell transplant outcomes

A Pilot Study of Nicotinamide Riboside Supplementation in Allogeneic Hematopoietic Cell Transplantation

Early Phase 1 Interventional Case Comprehensive Cancer Center · NCT04332341

This study is testing if taking nicotinamide riboside can help patients who receive a stem cell transplant recover faster and have fewer complications.

Quick facts

PhaseEarly Phase 1
Study typeInterventional
Enrollment20 (estimated)
Ages18 Years and up
SexAll
SponsorCase Comprehensive Cancer Center Academic / other
Locations1 site (Cleveland, Ohio)
Trial IDNCT04332341 on ClinicalTrials.gov

What this trial studies

This pilot feasibility study investigates the safety and tolerability of nicotinamide riboside (NR) supplementation in patients undergoing allogeneic hematopoietic cell transplantation (HCT). The study aims to determine if increasing NAD+ levels through NR can enhance engraftment, which is the process where transplanted stem cells grow in the bone marrow and produce new blood cells. By potentially shortening the time to engraftment, the study seeks to reduce the risks associated with prolonged recovery periods, such as the need for transfusions and antibiotics. Participants will receive NR supplementation and be monitored for neutrophil and platelet recovery post-transplant.

Who should consider this trial

Good fit: Ideal candidates include individuals scheduled for allogeneic hematopoietic cell transplantation who meet specific eligibility criteria.

Not a fit: Patients with a history of allergy to NR compounds or those who are pregnant or breastfeeding will not benefit from this study.

Why it matters

Potential benefit: If successful, this approach could lead to faster recovery times and improved health outcomes for patients undergoing stem cell transplants.

How similar studies have performed: While the approach of using nicotinamide riboside is relatively novel, preliminary studies suggest potential benefits in enhancing stem cell engraftment.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* All disease indications for allogeneic hematopoietic cell transplantation except for myelofibrosis.
* Subject must meet program eligibility criteria\* for myeloablative conditioning alloHCT and plan to undergo myeloablative conditioning.
* HLA-identical related donor or unrelated human donor source with bone marrow graft.
* Subjects must provide a written informed consent.

Exclusion Criteria:

* History of allergy or intolerance to NR precursor compounds, including niacin or nicotinamide
* Pregnant or breastfeeding women are excluded from this study since allogeneic HCT is a strict contraindication.
* Subjects with uncontrolled intercurrent illness or psychiatric illness/social situations that would limit compliance with study requirements.

Where this trial is running

Cleveland, Ohio

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Allogeneic Hematopoietic Cell Transplantation
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.