Long-term safety and effectiveness follow-up after gene-modified T cell treatment in adults

A Long-Term Follow-up Protocol for Participants Treated With Gene Modified T Cells

Observational Regeneron Pharmaceuticals · NCT06798298

This follows adults who received gene-modified T cell therapy to see whether the treatment stays safe and continues to work over the long term.

Quick facts

Study typeObservational
Enrollment50 (estimated)
Ages18 Years and up
SexAll
SponsorRegeneron Pharmaceuticals Industry-sponsored
Locations1 site (Nashville, Tennessee)
Trial IDNCT06798298 on ClinicalTrials.gov

What this trial studies

This prospective long-term follow-up protocol enrolls adults previously treated with gene-modified T cells in Regeneron- or 2seventy bio–sponsored studies. Eligible participants received at least one infusion and have completed or discontinued their parent protocol after the required post-treatment monitoring. The study is non-interventional and collects scheduled safety assessments, laboratory tests, and patient-reported outcome questionnaires over time in accordance with health authority guidance. Follow-up includes monitoring for replication-competent lentivirus and other long-term safety or durability signals.

Who should consider this trial

Good fit: Adults who received at least one infusion of gene-modified T cells in a prior Regeneron or 2seventy bio–sponsored protocol and completed or discontinued the parent study after required monitoring are eligible.

Not a fit: People who never received gene-modified T cell therapy or who cannot attend required follow-up visits are not candidates and would not gain direct benefit from this protocol.

Why it matters

Potential benefit: If successful, the study could identify long-term safety issues or lasting benefits, helping clinicians counsel and manage future patients treated with gene-modified T cells.

How similar studies have performed: Long-term follow-up programs for gene-modified T cell therapies, including CAR-T products, have previously provided valuable safety and durability data, so this approach builds on established practice.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

1. All participants who received at least one GM T cell infusion in a previous 2seventy bio (prior to April 2024) or Regeneron Pharmaceuticals sponsored study, and have completed the post-treatment follow-up period on the parent treatment protocol, or discontinued follow-up on the parent protocol after completing at least 6 months of safety monitoring, as applicable.
2. Participant (and legal representative, when applicable) must understand and voluntarily sign an Informed Consent Form (ICF)/Informed Assent Form (IAF) prior to any study related assessments/procedures being conducted.

Exclusion Criteria:

Not applicable.

Where this trial is running

Nashville, Tennessee

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Long Term Safety Following GM T Cell TherapyGM T cell therapyReplication Competent Lentivirus
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.