Investigating ALN-APOC3 for treating dyslipidemia in adults

A Phase 1/2a, Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ALN-APOC3 in Adult Participants With Dyslipidemia

Phase1; Phase2 Interventional Regeneron Pharmaceuticals · NCT06784349

This study is testing a new drug called ALN-APOC3 to see if it can safely help adults with abnormal blood lipid levels improve their health.

Quick facts

PhasePhase1; Phase2
Study typeInterventional
Enrollment136 (estimated)
Ages18 Years to 75 Years
SexAll
SponsorRegeneron Pharmaceuticals Industry-sponsored
Locations1 site (Chisinau)
Trial IDNCT06784349 on ClinicalTrials.gov

What this trial studies

This study evaluates the safety and effectiveness of an experimental drug called ALN-APOC3 in adults with dyslipidemia, characterized by abnormal lipid levels in the blood. The trial is divided into two parts, with participants in Part A being excluded from Part B. Researchers will monitor side effects, measure drug levels in the blood, and assess changes in lipid levels over time. Participants must meet specific health criteria and lipid level thresholds to qualify for the study.

Who should consider this trial

Good fit: Ideal candidates are adults with dyslipidemia who are either not on statin therapy or are on a stable dose of statins.

Not a fit: Patients with significant cardiovascular or other serious health conditions may not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could provide a new therapeutic option for managing dyslipidemia and improving lipid profiles in patients.

How similar studies have performed: Other studies have shown promise with similar lipid-modifying therapies, indicating potential for success in this approach.

Eligibility criteria

Show full inclusion / exclusion criteria
Key Inclusion Criteria:

1. Judged by the investigator to be in in good health based on medical history, physical examination, vital signs, electrocardiograms (ECG's) and laboratory safety testing, as defined in the protocol
2. Participants can enter the study under one of the following options, as defined in the protocol:

   1. Currently not taking statin and have not been on statin therapy for the 3 months prior to screening, or
   2. On a stable dose of statin, taken continuously for 3 months
3. Fasting triglycerides concentrations ≥100 and \<500 mg/dL (1.13 to 5.65 mmol/L) during screening visit, as defined in the protocol
4. Fasting LDL-C ≥70 (1.81 mmol/L) if on stable statin therapy OR if not on statin treatment, as defined in the protocol

Key Exclusion Criteria:

1. History of clinically significant cardiovascular (other than dyslipidemia), respiratory, hepatic, renal, gastrointestinal, endocrine, hematological, psychiatric, or neurological disease, or any other concern, as assessed by the investigator that may confound the results of the study or poses an additional risk to the participant by study participation
2. Was hospitalized (ie, \>24 hours) for any reason within 30 days of the screening visit
3. Is positive for human immunodeficiency virus (HIV) or hepatitis B surface antigen (HBsAg) at the screening visit, as defined in the protocol
4. Is positive for hepatitis C antibody and positive for qualitative hepatitis c virus (HCV) ribonucleic acid (RNA) test at the screening visit
5. Any malignancy, except for non-melanoma skin cancer or cervical/anus in-situ, that have been resected with no evidence of metastatic disease for 3 years prior to the screening visit

NOTE: Other protocol defined inclusion/exclusion criteria apply

Where this trial is running

Chisinau

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions DyslipidemiaLipidsTriglyceridesCholesterol
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.